{"id":"https://openalex.org/W908639680","doi":null,"title":"Characterization Of A Novel Gene Therapy Reporter Vector (rAAV2/5-CBA-CNGA3-IRES-GFP) In A Mouse Model Of Achromatopsia","display_name":"Characterization Of A Novel Gene Therapy Reporter Vector (rAAV2/5-CBA-CNGA3-IRES-GFP) In A Mouse Model Of Achromatopsia","publication_year":2012,"publication_date":"2012-03-26","ids":{"openalex":"https://openalex.org/W908639680","mag":"908639680"},"language":"en","primary_location":{"id":"mag:908639680","doi":null,"is_oa":false,"landing_page_url":"https://iovs.arvojournals.org/article.aspx?articleid=2351899","pdf_url":null,"source":{"id":"https://openalex.org/S76304953","display_name":"Investigative Ophthalmology & Visual Science","issn_l":"0146-0404","issn":["0146-0404","1552-5783"],"is_oa":false,"is_in_doaj":true,"is_core":true,"listed_in":["anvur-scientific","cwts-core","doaj","dongbi-c","doyens","jufo-2","ki-jl-2","medline","norway-2","oarl","poland-140","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310321950","host_organization_name":"Cadmus Press","host_organization_lineage":["https://openalex.org/P4310321950"],"host_organization_lineage_names":["Cadmus Press"],"type":"journal"},"license":null,"license_id":null,"version":null,"is_accepted":false,"is_published":false,"raw_source_name":"Investigative Ophthalmology & Visual Science","raw_type":null},"volume":null,"type":"article","is_traditional":true,"indexed_in":[],"open_access":{"is_oa":false,"oa_status":"closed","oa_url":null,"any_repository_has_fulltext":false},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5059732404","display_name":"Srini Goverdhan","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I40120149","display_name":"University of Oxford","ror":"https://ror.org/052gg0110","country_code":"GB","type":"education","lineage":["https://openalex.org/I40120149"]},{"id":"https://openalex.org/I43439940","display_name":"University of Southampton","ror":"https://ror.org/01ryk1543","country_code":"GB","type":"education","lineage":["https://openalex.org/I43439940"]}],"countries":["GB"],"is_corresponding":false,"raw_author_name":"Srini Goverdhan","raw_affiliation_strings":["Nuffield Laboratory of Ophthalmology, University of Oxford, Oxford, United Kingdom","Vision Research Group / Southampton Eye Unit, University of Southampton, Southampton, United Kingdom"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Nuffield Laboratory of Ophthalmology, University of Oxford, Oxford, United Kingdom","institution_ids":["https://openalex.org/I40120149"]},{"raw_affiliation_string":"Vision Research Group / Southampton Eye Unit, University of Southampton, Southampton, United Kingdom","institution_ids":["https://openalex.org/I43439940"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5055338875","display_name":"Alun R. Barnard","orcid":"https://orcid.org/0000-0002-0662-1073","observed_orcids":["https://orcid.org/0000-0002-0662-1073"]},"institutions":[{"id":"https://openalex.org/I40120149","display_name":"University of Oxford","ror":"https://ror.org/052gg0110","country_code":"GB","type":"education","lineage":["https://openalex.org/I40120149"]}],"countries":["GB"],"is_corresponding":false,"raw_author_name":"Alun R. Barnard","raw_affiliation_strings":["Nuffield Laboratory Of Ophthalmology, University OF Oxford, Oxford, United Kingdom"],"raw_orcid":"https://orcid.org/0000-0002-0662-1073","affiliations":[{"raw_affiliation_string":"Nuffield Laboratory Of Ophthalmology, University OF Oxford, Oxford, United Kingdom","institution_ids":["https://openalex.org/I40120149"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5075781178","display_name":"Mandeep S. Singh","orcid":"https://orcid.org/0000-0003-1749-0088","observed_orcids":["https://orcid.org/0000-0003-1749-0088"]},"institutions":[{"id":"https://openalex.org/I40120149","display_name":"University of Oxford","ror":"https://ror.org/052gg0110","country_code":"GB","type":"education","lineage":["https://openalex.org/I40120149"]}],"countries":["GB"],"is_corresponding":false,"raw_author_name":"Mandeep S. Singh","raw_affiliation_strings":["Nuffield Laboratory Of Ophthalmology, University OF Oxford, Oxford, United Kingdom"],"raw_orcid":"https://orcid.org/0000-0003-1749-0088","affiliations":[{"raw_affiliation_string":"Nuffield Laboratory Of Ophthalmology, University OF Oxford, Oxford, United Kingdom","institution_ids":["https://openalex.org/I40120149"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5073328427","display_name":"Peter Charbel Issa","orcid":"https://orcid.org/0000-0002-0351-6673","observed_orcids":["https://orcid.org/0000-0002-0351-6673"]},"institutions":[{"id":"https://openalex.org/I40120149","display_name":"University of Oxford","ror":"https://ror.org/052gg0110","country_code":"GB","type":"education","lineage":["https://openalex.org/I40120149"]}],"countries":["GB"],"is_corresponding":false,"raw_author_name":"Peter Charbel Issa","raw_affiliation_strings":["Nuffield Laboratory Of Ophthalmology, University OF Oxford, Oxford, United Kingdom"],"raw_orcid":"https://orcid.org/0000-0002-0351-6673","affiliations":[{"raw_affiliation_string":"Nuffield Laboratory Of Ophthalmology, University OF Oxford, Oxford, United Kingdom","institution_ids":["https://openalex.org/I40120149"]}]},{"author_position":"last","author":{"id":"https://openalex.org/A5046326117","display_name":"Robert Edward MacLaren","orcid":"https://orcid.org/0000-0002-3096-4682","observed_orcids":["https://orcid.org/0000-0002-3096-4682","https://orcid.org/0009-0001-5561-1365"]},"institutions":[{"id":"https://openalex.org/I1325675289","display_name":"Moorfields Eye Hospital NHS Foundation Trust","ror":"https://ror.org/03zaddr67","country_code":"GB","type":"healthcare","lineage":["https://openalex.org/I1325675289"]},{"id":"https://openalex.org/I40120149","display_name":"University of Oxford","ror":"https://ror.org/052gg0110","country_code":"GB","type":"education","lineage":["https://openalex.org/I40120149"]}],"countries":["GB"],"is_corresponding":false,"raw_author_name":"Robert E. MacLaren","raw_affiliation_strings":["Nuffield Laboratory of Ophthalmology, University of Oxford, Oxford, United Kingdom","Moorfields Eye Hospital NHS Foundation Trust, London, United Kingdom"],"raw_orcid":"https://orcid.org/0000-0002-3096-4682","affiliations":[{"raw_affiliation_string":"Nuffield Laboratory of Ophthalmology, University of Oxford, Oxford, United Kingdom","institution_ids":["https://openalex.org/I40120149"]},{"raw_affiliation_string":"Moorfields Eye Hospital NHS Foundation Trust, London, United Kingdom","institution_ids":["https://openalex.org/I1325675289"]}]}],"institutions":[],"countries_distinct_count":1,"institutions_distinct_count":3,"corresponding_author_ids":[],"corresponding_institution_ids":[],"apc_list":{"value":1850,"currency":"USD","value_usd":1850},"apc_paid":null,"fwci":0.0,"has_fulltext":false,"cited_by_count":0,"citation_normalized_percentile":{"value":0.1038794,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":null,"biblio":{"volume":"53","issue":"14","first_page":"1921","last_page":"1921"},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T10691","display_name":"Retinal Development and Disorders","score":0.9702000021934509,"subfield":{"id":"https://openalex.org/subfields/2731","display_name":"Ophthalmology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},"topics":[{"id":"https://openalex.org/T10691","display_name":"Retinal Development and Disorders","score":0.9702000021934509,"subfield":{"id":"https://openalex.org/subfields/2731","display_name":"Ophthalmology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T10613","display_name":"Virus-based gene therapy research","score":0.024800000712275505,"subfield":{"id":"https://openalex.org/subfields/1311","display_name":"Genetics"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},{"id":"https://openalex.org/T10725","display_name":"RNA Interference and Gene Delivery","score":0.0008999999845400453,"subfield":{"id":"https://openalex.org/subfields/1312","display_name":"Molecular Biology"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/cnga3","display_name":"CNGA3","score":0.8339999914169312},{"id":"https://openalex.org/keywords/cyclic-nucleotide-gated-channels","display_name":"cyclic nucleotide-gated channels","score":0.7820000052452087},{"id":"https://openalex.org/keywords/achromatopsia","display_name":"achromatopsia","score":0.8410000205039978},{"id":"https://openalex.org/keywords/mouse-model","display_name":"mouse model","score":0.8489999771118164},{"id":"https://openalex.org/keywords/retinal-gene-therapy","display_name":"retinal gene therapy","score":0.6129999756813049}],"concepts":[{"id":"https://openalex.org/C2777906962","wikidata":"https://www.wikidata.org/wiki/Q432396","display_name":"Achromatopsia","level":3,"score":0.8846274018287659},{"id":"https://openalex.org/C142613039","wikidata":"https://www.wikidata.org/wiki/Q272983","display_name":"Green fluorescent protein","level":3,"score":0.650611400604248},{"id":"https://openalex.org/C92087593","wikidata":"https://www.wikidata.org/wiki/Q427389","display_name":"Vector (molecular biology)","level":4,"score":0.6326313018798828},{"id":"https://openalex.org/C161733203","wikidata":"https://www.wikidata.org/wiki/Q911828","display_name":"Reporter gene","level":4,"score":0.5537902116775513},{"id":"https://openalex.org/C86803240","wikidata":"https://www.wikidata.org/wiki/Q420","display_name":"Biology","level":0,"score":0.507808268070221},{"id":"https://openalex.org/C111599444","wikidata":"https://www.wikidata.org/wiki/Q213901","display_name":"Genetic enhancement","level":3,"score":0.49559009075164795},{"id":"https://openalex.org/C153911025","wikidata":"https://www.wikidata.org/wiki/Q7202","display_name":"Molecular biology","level":1,"score":0.4297231137752533},{"id":"https://openalex.org/C104317684","wikidata":"https://www.wikidata.org/wiki/Q7187","display_name":"Gene","level":2,"score":0.3610452711582184},{"id":"https://openalex.org/C54355233","wikidata":"https://www.wikidata.org/wiki/Q7162","display_name":"Genetics","level":1,"score":0.2879549264907837},{"id":"https://openalex.org/C150194340","wikidata":"https://www.wikidata.org/wiki/Q26972","display_name":"Gene expression","level":3,"score":0.1452772617340088},{"id":"https://openalex.org/C40767141","wikidata":"https://www.wikidata.org/wiki/Q285697","display_name":"Recombinant DNA","level":3,"score":0.13074493408203125},{"id":"https://openalex.org/C55493867","wikidata":"https://www.wikidata.org/wiki/Q7094","display_name":"Biochemistry","level":1,"score":0.042295247316360474},{"id":"https://openalex.org/C2780827179","wikidata":"https://www.wikidata.org/wiki/Q422001","display_name":"Retinal","level":2,"score":0.0}],"mesh":[],"locations_count":1,"locations":[{"id":"mag:908639680","doi":null,"is_oa":false,"landing_page_url":"https://iovs.arvojournals.org/article.aspx?articleid=2351899","pdf_url":null,"source":{"id":"https://openalex.org/S76304953","display_name":"Investigative Ophthalmology & Visual Science","issn_l":"0146-0404","issn":["0146-0404","1552-5783"],"is_oa":false,"is_in_doaj":true,"is_core":true,"listed_in":["anvur-scientific","cwts-core","doaj","dongbi-c","doyens","jufo-2","ki-jl-2","medline","norway-2","oarl","poland-140","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310321950","host_organization_name":"Cadmus Press","host_organization_lineage":["https://openalex.org/P4310321950"],"host_organization_lineage_names":["Cadmus Press"],"type":"journal"},"license":null,"license_id":null,"version":null,"is_accepted":false,"is_published":false,"raw_source_name":"Investigative Ophthalmology & Visual Science","raw_type":null}],"best_oa_location":null,"sustainable_development_goals":[{"score":0.8048999905586243,"display_name":"Good health and well-being","id":"https://metadata.un.org/sdg/3"}],"study_designs":[],"awards":[],"funders":[],"has_content":{"pdf":false,"grobid_xml":false},"content_urls":null,"referenced_works_count":0,"referenced_works":[],"related_works":["https://openalex.org/W1900084868","https://openalex.org/W1173214725","https://openalex.org/W947418538","https://openalex.org/W854480329","https://openalex.org/W1015201087","https://openalex.org/W873681351","https://openalex.org/W2571564289","https://openalex.org/W2790065554","https://openalex.org/W2046026739","https://openalex.org/W772181471"],"abstract_inverted_index":null,"counts_by_year":[],"updated_date":"2026-09-26T08:19:03.415552","created_date":"2016-06-24T00:00:00"}
