{"id":"https://openalex.org/W7225323252","doi":"https://doi.org/10.1186/s13023-026-04694-8","title":"Validation of the 7-day FABPRO-GI questionnaire in Turkish Fabry disease patients","display_name":"Validation of the 7-day FABPRO-GI questionnaire in Turkish Fabry disease patients","publication_year":2026,"publication_date":"2026-11-06","ids":{"openalex":"https://openalex.org/W7225323252","doi":"https://doi.org/10.1186/s13023-026-04694-8"},"language":"en","primary_location":{"id":"doi:10.1186/s13023-026-04694-8","doi":"https://doi.org/10.1186/s13023-026-04694-8","is_oa":true,"landing_page_url":"https://doi.org/10.1186/s13023-026-04694-8","pdf_url":null,"source":{"id":"https://openalex.org/S71291065","display_name":"Orphanet Journal of Rare Diseases","issn_l":"1750-1172","issn":["1750-1172"],"is_oa":true,"is_in_doaj":true,"is_core":true,"listed_in":["anvur-scientific","cwts-core","doaj","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","oarl","poland-100","russia-white-list-2","vabb-shw"],"host_organization":"https://openalex.org/P4310320256","host_organization_name":"BioMed Central","host_organization_lineage":["https://openalex.org/P4310320256","https://openalex.org/P4310319965"],"host_organization_lineage_names":["BioMed Central","Springer Nature"],"type":"journal"},"license":"cc-by","license_id":"https://openalex.org/licenses/cc-by","version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Orphanet Journal of Rare Diseases","raw_type":"journal-article"},"volume":null,"type":"article","is_traditional":true,"indexed_in":["crossref","doaj"],"open_access":{"is_oa":true,"oa_status":"gold","oa_url":"https://doi.org/10.1186/s13023-026-04694-8","any_repository_has_fulltext":false},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5018247370","display_name":"\u015eeyda G\u00fcl \u00d6zcan","orcid":"https://orcid.org/0000-0002-4341-5252","observed_orcids":["https://orcid.org/0000-0002-4341-5252"]},"institutions":[{"id":"https://openalex.org/I4210112471","display_name":"Istanbul University-Cerrahpa\u015fa","ror":"https://ror.org/01dzn5f42","country_code":"TR","type":"education","lineage":["https://openalex.org/I4210112471"]}],"countries":["TR"],"is_corresponding":true,"raw_author_name":"Seyda Gul Ozcan","raw_affiliation_strings":["Department of Nephrology, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey"],"raw_orcid":"https://orcid.org/0000-0002-4341-5252","affiliations":[{"raw_affiliation_string":"Department of Nephrology, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey","institution_ids":["https://openalex.org/I4210112471"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5003132118","display_name":"Necmi Eren","orcid":"https://orcid.org/0000-0002-2708-3470","observed_orcids":["https://orcid.org/0000-0002-2708-3470"]},"institutions":[{"id":"https://openalex.org/I51826884","display_name":"Kocaeli \u00dcniversitesi","ror":"https://ror.org/0411seq30","country_code":"TR","type":"education","lineage":["https://openalex.org/I51826884"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"Necmi Eren","raw_affiliation_strings":["Department of Nephrology, Kocaeli Medical Faculty, Kocaeli University, Kocaeli, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Department of Nephrology, Kocaeli Medical Faculty, Kocaeli University, Kocaeli, Turkey","institution_ids":["https://openalex.org/I51826884"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5160915450","display_name":"Melis Atakan","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I4210112471","display_name":"Istanbul University-Cerrahpa\u015fa","ror":"https://ror.org/01dzn5f42","country_code":"TR","type":"education","lineage":["https://openalex.org/I4210112471"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"Melis Atakan","raw_affiliation_strings":["Department of Internal Medicine, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Department of Internal Medicine, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey","institution_ids":["https://openalex.org/I4210112471"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5160824012","display_name":"Talha Soyeri","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I51826884","display_name":"Kocaeli \u00dcniversitesi","ror":"https://ror.org/0411seq30","country_code":"TR","type":"education","lineage":["https://openalex.org/I51826884"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"Talha Soyeri","raw_affiliation_strings":["Department of Internal Medicine, Kocaeli Medical Faculty, Kocaeli University, Kocaeli, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Department of Internal Medicine, Kocaeli Medical Faculty, Kocaeli University, Kocaeli, Turkey","institution_ids":["https://openalex.org/I51826884"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5026992017","display_name":"Zeynep Atl\u0131","orcid":"https://orcid.org/0000-0002-2959-0978","observed_orcids":["https://orcid.org/0000-0002-2959-0978"]},"institutions":[{"id":"https://openalex.org/I76257594","display_name":"Sinop University","ror":"https://ror.org/004ah3r71","country_code":"TR","type":"education","lineage":["https://openalex.org/I76257594"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"Zeynep Atli","raw_affiliation_strings":["Department of Data Science and Analytics, Faculty of Science and Letters, Sinop University, Sinop, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Department of Data Science and Analytics, Faculty of Science and Letters, Sinop University, Sinop, Turkey","institution_ids":["https://openalex.org/I76257594"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5078483635","display_name":"Mevl\u00fct Tamer Din\u00e7er","orcid":"https://orcid.org/0000-0002-5397-7697","observed_orcids":["https://orcid.org/0000-0002-5397-7697"]},"institutions":[{"id":"https://openalex.org/I4210112471","display_name":"Istanbul University-Cerrahpa\u015fa","ror":"https://ror.org/01dzn5f42","country_code":"TR","type":"education","lineage":["https://openalex.org/I4210112471"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"Mevlut Tamer Dincer","raw_affiliation_strings":["Department of Nephrology, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Department of Nephrology, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey","institution_ids":["https://openalex.org/I4210112471"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5069052018","display_name":"Sinan Trabulus","orcid":"https://orcid.org/0000-0003-3843-5950","observed_orcids":["https://orcid.org/0000-0003-3843-5950"]},"institutions":[{"id":"https://openalex.org/I4210112471","display_name":"Istanbul University-Cerrahpa\u015fa","ror":"https://ror.org/01dzn5f42","country_code":"TR","type":"education","lineage":["https://openalex.org/I4210112471"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"Sinan Trabulus","raw_affiliation_strings":["Department of Nephrology, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Department of Nephrology, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey","institution_ids":["https://openalex.org/I4210112471"]}]},{"author_position":"last","author":{"id":"https://openalex.org/A5013481330","display_name":"Nurhan Seyahi","orcid":"https://orcid.org/0000-0001-7427-618X","observed_orcids":["https://orcid.org/0000-0001-7427-618X"]},"institutions":[{"id":"https://openalex.org/I4210112471","display_name":"Istanbul University-Cerrahpa\u015fa","ror":"https://ror.org/01dzn5f42","country_code":"TR","type":"education","lineage":["https://openalex.org/I4210112471"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"Nurhan Seyahi","raw_affiliation_strings":["Department of Nephrology, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Department of Nephrology, Cerrahpasa Medical Faculty, Istanbul University-Cerrahpasa, Istanbul, Turkey","institution_ids":["https://openalex.org/I4210112471"]}]}],"institutions":[],"countries_distinct_count":1,"institutions_distinct_count":3,"corresponding_author_ids":["https://openalex.org/A5018247370"],"corresponding_institution_ids":["https://openalex.org/I4210112471"],"apc_list":{"value":2990,"currency":"USD","value_usd":2990},"apc_paid":{"value":2990,"currency":"USD","value_usd":2990},"fwci":0.0,"has_fulltext":false,"cited_by_count":0,"citation_normalized_percentile":{"value":0.0,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":null,"biblio":{"volume":null,"issue":null,"first_page":null,"last_page":null},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T10945","display_name":"Lysosomal Storage Disorders Research","score":0.9955999851226807,"subfield":{"id":"https://openalex.org/subfields/2716","display_name":"Genetics (clinical)"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},"topics":[{"id":"https://openalex.org/T10945","display_name":"Lysosomal Storage Disorders Research","score":0.9955999851226807,"subfield":{"id":"https://openalex.org/subfields/2716","display_name":"Genetics (clinical)"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T13117","display_name":"Health Education and Validation","score":0.0027000000700354576,"subfield":{"id":"https://openalex.org/subfields/2922","display_name":"Research and Theory"},"field":{"id":"https://openalex.org/fields/29","display_name":"Nursing"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T10365","display_name":"Gastrointestinal motility and disorders","score":0.00039999998989515007,"subfield":{"id":"https://openalex.org/subfields/2715","display_name":"Gastroenterology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/fabry-disease","display_name":"Fabry disease","score":0.9990000128746033},{"id":"https://openalex.org/keywords/gastrointestinal-symptoms","display_name":"gastrointestinal symptoms","score":0.8500000238418579},{"id":"https://openalex.org/keywords/patient-reported-outcome-measures","display_name":"patient-reported outcome measures","score":0.6660000085830688},{"id":"https://openalex.org/keywords/psychometric-validation","display_name":"psychometric validation","score":0.8479999899864197},{"id":"https://openalex.org/keywords/turkish-translation","display_name":"Turkish translation","score":0.8240000009536743},{"id":"https://openalex.org/keywords/gastrointestinal-symptom-rating-scale","display_name":"Gastrointestinal Symptom Rating Scale","score":0.8690000176429749},{"id":"https://openalex.org/keywords/quality-of-life","display_name":"quality of life","score":0.6549999713897705},{"id":"https://openalex.org/keywords/lyso-gb3","display_name":"lyso-Gb3","score":0.7269999980926514},{"id":"https://openalex.org/keywords/internal-consistency","display_name":"internal consistency","score":0.5759999752044678},{"id":"https://openalex.org/keywords/convergent-and-discriminant-validity","display_name":"convergent and discriminant validity","score":0.8489999771118164}],"concepts":[{"id":"https://openalex.org/C2781121862","wikidata":"https://www.wikidata.org/wiki/Q256","display_name":"Turkish","level":2,"score":0.6442999839782715},{"id":"https://openalex.org/C120107772","wikidata":"https://www.wikidata.org/wiki/Q168554","display_name":"Discriminant validity","level":4,"score":0.6270999908447266},{"id":"https://openalex.org/C121244757","wikidata":"https://www.wikidata.org/wiki/Q1783487","display_name":"Convergent validity","level":4,"score":0.5932000279426575},{"id":"https://openalex.org/C49453240","wikidata":"https://www.wikidata.org/wiki/Q1592163","display_name":"Construct validity","level":3,"score":0.5756000280380249},{"id":"https://openalex.org/C83849319","wikidata":"https://www.wikidata.org/wiki/Q7295720","display_name":"Rating scale","level":2,"score":0.4941999912261963},{"id":"https://openalex.org/C71924100","wikidata":"https://www.wikidata.org/wiki/Q11190","display_name":"Medicine","level":0,"score":0.46639999747276306},{"id":"https://openalex.org/C117220453","wikidata":"https://www.wikidata.org/wiki/Q5172842","display_name":"Correlation","level":2,"score":0.44850000739097595},{"id":"https://openalex.org/C2781112942","wikidata":"https://www.wikidata.org/wiki/Q178436","display_name":"Constipation","level":2,"score":0.4357999861240387},{"id":"https://openalex.org/C2776035688","wikidata":"https://www.wikidata.org/wiki/Q1606558","display_name":"Affect (linguistics)","level":2,"score":0.4221999943256378},{"id":"https://openalex.org/C171606756","wikidata":"https://www.wikidata.org/wiki/Q506132","display_name":"Psychometrics","level":2,"score":0.4198000133037567},{"id":"https://openalex.org/C3018868096","wikidata":"https://www.wikidata.org/wiki/Q2693233","display_name":"Internal consistency","level":3,"score":0.4097999930381775},{"id":"https://openalex.org/C2779951463","wikidata":"https://www.wikidata.org/wiki/Q7268788","display_name":"Quality of life (healthcare)","level":2,"score":0.4088999927043915},{"id":"https://openalex.org/C126322002","wikidata":"https://www.wikidata.org/wiki/Q11180","display_name":"Internal medicine","level":1,"score":0.3912000060081482},{"id":"https://openalex.org/C2778755073","wikidata":"https://www.wikidata.org/wiki/Q10858537","display_name":"Scale (ratio)","level":2,"score":0.37959998846054077},{"id":"https://openalex.org/C70410870","wikidata":"https://www.wikidata.org/wiki/Q199906","display_name":"Clinical psychology","level":1,"score":0.3700000047683716},{"id":"https://openalex.org/C15744967","wikidata":"https://www.wikidata.org/wiki/Q9418","display_name":"Psychology","level":0,"score":0.3544999957084656},{"id":"https://openalex.org/C198999979","wikidata":"https://www.wikidata.org/wiki/Q5159115","display_name":"Concurrent validity","level":4,"score":0.3375999927520752},{"id":"https://openalex.org/C71104824","wikidata":"https://www.wikidata.org/wiki/Q1476639","display_name":"Structural equation modeling","level":2,"score":0.329800009727478},{"id":"https://openalex.org/C19875794","wikidata":"https://www.wikidata.org/wiki/Q1207340","display_name":"Item response theory","level":3,"score":0.3294000029563904},{"id":"https://openalex.org/C30036603","wikidata":"https://www.wikidata.org/wiki/Q17125150","display_name":"Severity of illness","level":2,"score":0.30880001187324524},{"id":"https://openalex.org/C70364389","wikidata":"https://www.wikidata.org/wiki/Q18757","display_name":"Validity","level":3,"score":0.3084999918937683},{"id":"https://openalex.org/C2779134260","wikidata":"https://www.wikidata.org/wiki/Q12136","display_name":"Disease","level":2,"score":0.30000001192092896},{"id":"https://openalex.org/C40722632","wikidata":"https://www.wikidata.org/wiki/Q5160137","display_name":"Confirmatory factor analysis","level":3,"score":0.2831999957561493},{"id":"https://openalex.org/C116211729","wikidata":"https://www.wikidata.org/wiki/Q5372350","display_name":"Test validity","level":3,"score":0.27059999108314514},{"id":"https://openalex.org/C43214815","wikidata":"https://www.wikidata.org/wiki/Q7310987","display_name":"Reliability (semiconductor)","level":3,"score":0.263700008392334},{"id":"https://openalex.org/C182050348","wikidata":"https://www.wikidata.org/wiki/Q5186576","display_name":"Criterion validity","level":4,"score":0.26109999418258667},{"id":"https://openalex.org/C2778263599","wikidata":"https://www.wikidata.org/wiki/Q1669245","display_name":"Item analysis","level":3,"score":0.2563000023365021},{"id":"https://openalex.org/C1862650","wikidata":"https://www.wikidata.org/wiki/Q186005","display_name":"Physical therapy","level":1,"score":0.2558000087738037}],"mesh":[],"locations_count":1,"locations":[{"id":"doi:10.1186/s13023-026-04694-8","doi":"https://doi.org/10.1186/s13023-026-04694-8","is_oa":true,"landing_page_url":"https://doi.org/10.1186/s13023-026-04694-8","pdf_url":null,"source":{"id":"https://openalex.org/S71291065","display_name":"Orphanet Journal of Rare Diseases","issn_l":"1750-1172","issn":["1750-1172"],"is_oa":true,"is_in_doaj":true,"is_core":true,"listed_in":["anvur-scientific","cwts-core","doaj","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","oarl","poland-100","russia-white-list-2","vabb-shw"],"host_organization":"https://openalex.org/P4310320256","host_organization_name":"BioMed Central","host_organization_lineage":["https://openalex.org/P4310320256","https://openalex.org/P4310319965"],"host_organization_lineage_names":["BioMed Central","Springer Nature"],"type":"journal"},"license":"cc-by","license_id":"https://openalex.org/licenses/cc-by","version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Orphanet Journal of Rare Diseases","raw_type":"journal-article"}],"best_oa_location":{"id":"doi:10.1186/s13023-026-04694-8","doi":"https://doi.org/10.1186/s13023-026-04694-8","is_oa":true,"landing_page_url":"https://doi.org/10.1186/s13023-026-04694-8","pdf_url":null,"source":{"id":"https://openalex.org/S71291065","display_name":"Orphanet Journal of Rare Diseases","issn_l":"1750-1172","issn":["1750-1172"],"is_oa":true,"is_in_doaj":true,"is_core":true,"listed_in":["anvur-scientific","cwts-core","doaj","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","oarl","poland-100","russia-white-list-2","vabb-shw"],"host_organization":"https://openalex.org/P4310320256","host_organization_name":"BioMed Central","host_organization_lineage":["https://openalex.org/P4310320256","https://openalex.org/P4310319965"],"host_organization_lineage_names":["BioMed Central","Springer Nature"],"type":"journal"},"license":"cc-by","license_id":"https://openalex.org/licenses/cc-by","version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Orphanet Journal of Rare Diseases","raw_type":"journal-article"},"sustainable_development_goals":[{"id":"https://metadata.un.org/sdg/3","score":1.0,"display_name":"Good health and well-being"}],"study_designs":[{"id":"https://openalex.org/study-designs/observational-study","display_name":"Observational Study"}],"awards":[],"funders":[],"has_content":{"grobid_xml":false,"pdf":false},"content_urls":null,"referenced_works_count":0,"referenced_works":[],"related_works":["https://openalex.org/W3159234670","https://openalex.org/W3216198655","https://openalex.org/W2912236611","https://openalex.org/W4416392355","https://openalex.org/W4210647949","https://openalex.org/W3173692265","https://openalex.org/W4410242283","https://openalex.org/W2118558603","https://openalex.org/W4210337561","https://openalex.org/W4283521033"],"abstract_inverted_index":{"Abstract":[0],"Background":[1],"Gastrointestinal":[2,92],"(GI)":[3],"symptoms":[4,36],"affect":[5],"over":[6],"50%":[7],"of":[8,18,56,60,174,236,255],"patients":[9,71,266],"with":[10,72,112,221,267],"Fabry":[11,268],"disease":[12],"(FD)":[13],"and":[14,90,108,118,146,149,157,179,192,230,243,272],"significantly":[15],"impair":[16],"quality":[17],"life.":[19],"The":[20,124,233],"7-day":[21,62,83,238],"FABry":[22],"Disease":[23],"Patient-Reported":[24],"Outcome-Gastro":[25],"intestinal":[26],"(FABPRO-GI)":[27],"is":[28,247],"the":[29,53,57,61,81,91,172,237,248,256],"first":[30,249],"disease-specific":[31],"instrument":[32],"for":[33],"assessing":[34],"GI":[35],"in":[37,264],"FD.":[38],"However,":[39],"psychometric":[40,54,253],"validation":[41,67,254],"beyond":[42,258],"content":[43,259],"validity":[44,135,168],"has":[45],"not":[46],"been":[47],"published.":[48],"We":[49,101],"aimed":[50],"to":[51,251,274],"evaluate":[52],"properties":[55],"Turkish":[58,82,234,265],"version":[59,235],"FABPRO-GI.":[63],"Methods":[64],"This":[65,246],"cross-sectional":[66],"study":[68,250],"included":[69],"53":[70],"genetically":[73],"confirmed":[74],"FD":[75],"from":[76],"Turkey.":[77],"Participants":[78],"completed":[79],"both":[80],"FABPRO-GI":[84,125,144,156,177,193,216,239,257],"(8":[85],"severity":[86],"items,":[87],"0\u201310":[88],"scale)":[89],"Symptom":[93],"Rating":[94],"Scale":[95],"(GSRS;":[96],"5":[97],"domains,":[98],"1\u20137":[99],"scale).":[100],"assessed":[102],"internal":[103,128],"consistency,":[104],"floor/ceiling":[105],"effects,":[106],"convergent":[107],"discriminant":[109],"validity,":[110,260],"association":[111,200],"clinical":[113],"variables,":[114],"multiple":[115,214],"regression":[116],"analysis,":[117],"structural":[119,199],"equation":[120],"modeling":[121],"(SEM).":[122],"Results":[123],"demonstrated":[126],"excellent":[127,241],"consistency":[129],"(Cronbach\u2019s":[130],"alpha":[131],"=":[132,162,184,187,202,205],"0.904).":[133],"Convergent":[134],"was":[136,169,211],"supported":[137,170],"by":[138,150,171],"strong":[139,152,198],"correlations":[140],"between":[141,154,176],"conceptually":[142],"similar":[143],"items":[145],"GSRS":[147,158,180,191],"domains":[148],"a":[151,197],"correlation":[153,175],"total":[155],"scores":[159,217],"(":[160,182],"r":[161,183],"0.798,":[163],"p":[164,186,204],"<":[165],"0.001).":[166],"Discriminant":[167],"absence":[173],"constipation":[178],"diarrhea":[181],"0.018,":[185],"0.898).":[188],"In":[189,213],"SEM,":[190],"latent":[194],"factors":[195],"showed":[196],"(\u03b2":[201],"0.93,":[203],"0.002),":[206],"although":[207],"overall":[208],"model":[209],"fit":[210],"suboptimal.":[212],"regression,":[215],"were":[218],"independently":[219],"associated":[220],"potassium,":[222],"lyso-Gb3,":[223],"age,":[224],"diabetes,":[225],"triglycerides,":[226],"body":[227],"mass":[228],"index,":[229],"AST.":[231],"Conclusions":[232],"demonstrates":[240],"reliability":[242,271],"construct":[244],"validity.":[245],"provide":[252],"supporting":[261],"its":[262],"use":[263],"disease;":[269],"test-retest":[270],"responsiveness":[273],"change":[275],"require":[276],"further":[277],"evaluation.":[278],"Clinical":[279],"trial":[280],"number":[281],"Not":[282],"applicable.":[283]},"counts_by_year":[],"updated_date":"2026-11-07T11:25:07.637180","created_date":"2026-11-06T00:00:00"}
