{"id":"https://openalex.org/W7155489043","doi":"https://doi.org/10.1016/j.jtct.2026.04.026","title":"Eculizumab for Pediatric Hematopoietic Cell Transplant\u2013Associated Thrombotic Microangiopathy: Real-World Response Rates, Predictors of Poor Response, and an Optimal Time Point for Treatment Response Assessment","display_name":"Eculizumab for Pediatric Hematopoietic Cell Transplant\u2013Associated Thrombotic Microangiopathy: Real-World Response Rates, Predictors of Poor Response, and an Optimal Time Point for Treatment Response Assessment","publication_year":2026,"publication_date":"2026-04-24","ids":{"openalex":"https://openalex.org/W7155489043","doi":"https://doi.org/10.1016/j.jtct.2026.04.026","pmid":"https://pubmed.ncbi.nlm.nih.gov/42035874"},"language":"en","primary_location":{"id":"doi:10.1016/j.jtct.2026.04.026","doi":"https://doi.org/10.1016/j.jtct.2026.04.026","is_oa":false,"landing_page_url":"https://doi.org/10.1016/j.jtct.2026.04.026","pdf_url":null,"source":{"id":"https://openalex.org/S59987174","display_name":"Transplantation and Cellular Therapy","issn_l":"1083-8791","issn":["1083-8791","1523-6536","2666-6367"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","poland-100","poland-20","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Transplantation and Cellular Therapy","raw_type":"journal-article"},"volume":null,"type":"article","indexed_in":["crossref","pubmed"],"open_access":{"is_oa":false,"oa_status":"closed","oa_url":null,"any_repository_has_fulltext":false},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5046929879","display_name":"Michelle Long Schoettler","orcid":"https://orcid.org/0000-0003-4565-6399","observed_orcids":["https://orcid.org/0000-0003-4565-6399"]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]},{"id":"https://openalex.org/I4210146983","display_name":"Children's Healthcare of Atlanta","ror":"https://ror.org/050fhx250","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I4210146983"]}],"countries":["US"],"is_corresponding":true,"raw_author_name":"Michelle L. Schoettler","raw_affiliation_strings":["Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia. Electronic address: Michelle.Schoettler@emory.edu"],"raw_orcid":"https://orcid.org/0000-0003-4565-6399","affiliations":[{"raw_affiliation_string":"Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia. Electronic address: Michelle.Schoettler@emory.edu","institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5024406069","display_name":"Geoffrey Cheng","orcid":"https://orcid.org/0000-0002-6929-2502","observed_orcids":["https://orcid.org/0000-0002-6929-2502"]},"institutions":[{"id":"https://openalex.org/I180670191","display_name":"University of California, San Francisco","ror":"https://ror.org/043mz5j54","country_code":"US","type":"education","lineage":["https://openalex.org/I180670191"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Geoffrey Cheng","raw_affiliation_strings":["Division of Pediatric Allergy, Immunology, and Bone Marrow Transplant, University of California San Francisco, Benioff Children's Hospitals, San Francisco, California"],"raw_orcid":"https://orcid.org/0000-0002-6929-2502","affiliations":[{"raw_affiliation_string":"Division of Pediatric Allergy, Immunology, and Bone Marrow Transplant, University of California San Francisco, Benioff Children's Hospitals, San Francisco, California","institution_ids":["https://openalex.org/I180670191"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5086706731","display_name":"Christine S. Higham","orcid":"https://orcid.org/0000-0002-4618-3813","observed_orcids":["https://orcid.org/0000-0002-4618-3813"]},"institutions":[{"id":"https://openalex.org/I180670191","display_name":"University of California, San Francisco","ror":"https://ror.org/043mz5j54","country_code":"US","type":"education","lineage":["https://openalex.org/I180670191"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Christine S. Higham","raw_affiliation_strings":["Division of Pediatric Allergy, Immunology, and Bone Marrow Transplant, University of California San Francisco, Benioff Children's Hospitals, San Francisco, California"],"raw_orcid":"https://orcid.org/0000-0002-4618-3813","affiliations":[{"raw_affiliation_string":"Division of Pediatric Allergy, Immunology, and Bone Marrow Transplant, University of California San Francisco, Benioff Children's Hospitals, San Francisco, California","institution_ids":["https://openalex.org/I180670191"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5047178145","display_name":"Christopher C. Dvorak","orcid":"https://orcid.org/0000-0002-6146-3952","observed_orcids":["https://orcid.org/0000-0002-6146-3952"]},"institutions":[{"id":"https://openalex.org/I180670191","display_name":"University of California, San Francisco","ror":"https://ror.org/043mz5j54","country_code":"US","type":"education","lineage":["https://openalex.org/I180670191"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Christopher C. Dvorak","raw_affiliation_strings":["Division of Pediatric Allergy, Immunology, and Bone Marrow Transplant, University of California San Francisco, Benioff Children's Hospitals, San Francisco, California"],"raw_orcid":"https://orcid.org/0000-0002-6146-3952","affiliations":[{"raw_affiliation_string":"Division of Pediatric Allergy, Immunology, and Bone Marrow Transplant, University of California San Francisco, Benioff Children's Hospitals, San Francisco, California","institution_ids":["https://openalex.org/I180670191"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5158599562","display_name":"Cassandra Rush","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I1314135232","display_name":"Nationwide Children's Hospital","ror":"https://ror.org/003rfsp33","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1314135232"]},{"id":"https://openalex.org/I52357470","display_name":"The Ohio State University","ror":"https://ror.org/00rs6vg23","country_code":"US","type":"education","lineage":["https://openalex.org/I52357470"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Cassandra Rush","raw_affiliation_strings":["Department of Pediatric Hematology, Oncology, Blood and Marrow Transplant, Nationwide Children's Hospital, Columbus, Ohio and Department of Pediatrics, The Ohio State University, Columbus, Ohio"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Department of Pediatric Hematology, Oncology, Blood and Marrow Transplant, Nationwide Children's Hospital, Columbus, Ohio and Department of Pediatrics, The Ohio State University, Columbus, Ohio","institution_ids":["https://openalex.org/I1314135232","https://openalex.org/I52357470"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5062886533","display_name":"Hemalatha G. Rangarajan","orcid":"https://orcid.org/0000-0003-3371-2920","observed_orcids":["https://orcid.org/0000-0003-3371-2920"]},"institutions":[{"id":"https://openalex.org/I1314135232","display_name":"Nationwide Children's Hospital","ror":"https://ror.org/003rfsp33","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1314135232"]},{"id":"https://openalex.org/I52357470","display_name":"The Ohio State University","ror":"https://ror.org/00rs6vg23","country_code":"US","type":"education","lineage":["https://openalex.org/I52357470"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Hemalatha G. Rangarajan","raw_affiliation_strings":["Department of Pediatric Hematology, Oncology, Blood and Marrow Transplant, Nationwide Children's Hospital, Columbus, Ohio and Department of Pediatrics, The Ohio State University, Columbus, Ohio"],"raw_orcid":"https://orcid.org/0000-0003-3371-2920","affiliations":[{"raw_affiliation_string":"Department of Pediatric Hematology, Oncology, Blood and Marrow Transplant, Nationwide Children's Hospital, Columbus, Ohio and Department of Pediatrics, The Ohio State University, Columbus, Ohio","institution_ids":["https://openalex.org/I1314135232","https://openalex.org/I52357470"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5031543420","display_name":"Majed W. Al-Nazer","orcid":"https://orcid.org/0000-0002-6794-0860","observed_orcids":["https://orcid.org/0000-0002-6794-0860"]},"institutions":[{"id":"https://openalex.org/I1314135232","display_name":"Nationwide Children's Hospital","ror":"https://ror.org/003rfsp33","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1314135232"]},{"id":"https://openalex.org/I52357470","display_name":"The Ohio State University","ror":"https://ror.org/00rs6vg23","country_code":"US","type":"education","lineage":["https://openalex.org/I52357470"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Majed Al-Nazer","raw_affiliation_strings":["Department of Pediatric Hematology, Oncology, Blood and Marrow Transplant, Nationwide Children's Hospital, Columbus, Ohio and Department of Pediatrics, The Ohio State University, Columbus, Ohio"],"raw_orcid":"https://orcid.org/0000-0002-6794-0860","affiliations":[{"raw_affiliation_string":"Department of Pediatric Hematology, Oncology, Blood and Marrow Transplant, Nationwide Children's Hospital, Columbus, Ohio and Department of Pediatrics, The Ohio State University, Columbus, Ohio","institution_ids":["https://openalex.org/I1314135232","https://openalex.org/I52357470"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5006382432","display_name":"Veronika Polishchuk","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I1294278766","display_name":"Lurie Children's Hospital","ror":"https://ror.org/03a6zw892","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1294278766"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Veronika Polishchuk","raw_affiliation_strings":["Lurie Children's Hospital of Chicago, Chicago, Illinois"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Lurie Children's Hospital of Chicago, Chicago, Illinois","institution_ids":["https://openalex.org/I1294278766"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5073597251","display_name":"Sonali Chaudhury","orcid":"https://orcid.org/0000-0001-9816-5126","observed_orcids":["https://orcid.org/0000-0001-9816-5126"]},"institutions":[{"id":"https://openalex.org/I1294278766","display_name":"Lurie Children's Hospital","ror":"https://ror.org/03a6zw892","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1294278766"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Sonali Chaudhury","raw_affiliation_strings":["Lurie Children's Hospital of Chicago, Chicago, Illinois"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Lurie Children's Hospital of Chicago, Chicago, Illinois","institution_ids":["https://openalex.org/I1294278766"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5008479139","display_name":"Leslie Lehmann","orcid":"https://orcid.org/0000-0001-5558-4830","observed_orcids":["https://orcid.org/0000-0001-5558-4830"]},"institutions":[{"id":"https://openalex.org/I1288882113","display_name":"Boston Children's Hospital","ror":"https://ror.org/00dvg7y05","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1288882113"]},{"id":"https://openalex.org/I4210117453","display_name":"Dana-Farber Cancer Institute","ror":"https://ror.org/02jzgtq86","country_code":"US","type":"facility","lineage":["https://openalex.org/I4210117453"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Leslie Lehmann","raw_affiliation_strings":["Boston Children's Hospital, Dana Farber Cancer Institute, Boston, Massachusetts"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Boston Children's Hospital, Dana Farber Cancer Institute, Boston, Massachusetts","institution_ids":["https://openalex.org/I1288882113","https://openalex.org/I4210117453"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5110543173","display_name":"Christine Duncan","orcid":"https://orcid.org/0000-0002-2090-4897","observed_orcids":["https://orcid.org/0000-0002-2090-4897"]},"institutions":[{"id":"https://openalex.org/I1288882113","display_name":"Boston Children's Hospital","ror":"https://ror.org/00dvg7y05","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1288882113"]},{"id":"https://openalex.org/I4210117453","display_name":"Dana-Farber Cancer Institute","ror":"https://ror.org/02jzgtq86","country_code":"US","type":"facility","lineage":["https://openalex.org/I4210117453"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Christine Duncan","raw_affiliation_strings":["Boston Children's Hospital, Dana Farber Cancer Institute, Boston, Massachusetts"],"raw_orcid":"https://orcid.org/0000-0002-2090-4897","affiliations":[{"raw_affiliation_string":"Boston Children's Hospital, Dana Farber Cancer Institute, Boston, Massachusetts","institution_ids":["https://openalex.org/I1288882113","https://openalex.org/I4210117453"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5087776255","display_name":"Miki Nishitani","orcid":"https://orcid.org/0000-0001-9778-1197","observed_orcids":["https://orcid.org/0000-0001-9778-1197"]},"institutions":[{"id":"https://openalex.org/I1288882113","display_name":"Boston Children's Hospital","ror":"https://ror.org/00dvg7y05","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1288882113"]},{"id":"https://openalex.org/I4210117453","display_name":"Dana-Farber Cancer Institute","ror":"https://ror.org/02jzgtq86","country_code":"US","type":"facility","lineage":["https://openalex.org/I4210117453"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Miki Nishitani","raw_affiliation_strings":["Boston Children's Hospital, Dana Farber Cancer Institute, Boston, Massachusetts"],"raw_orcid":"https://orcid.org/0000-0001-9778-1197","affiliations":[{"raw_affiliation_string":"Boston Children's Hospital, Dana Farber Cancer Institute, Boston, Massachusetts","institution_ids":["https://openalex.org/I1288882113","https://openalex.org/I4210117453"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5116432314","display_name":"Haig Manougian","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I1316902750","display_name":"Cleveland Clinic","ror":"https://ror.org/03xjacd83","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1316902750"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Haig Manougian","raw_affiliation_strings":["Cleveland Clinic, Cleveland, Ohio"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Cleveland Clinic, Cleveland, Ohio","institution_ids":["https://openalex.org/I1316902750"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5004963644","display_name":"Seth R. Rotz","orcid":"https://orcid.org/0000-0003-2896-1113","observed_orcids":["https://orcid.org/0000-0003-2896-1113"]},"institutions":[{"id":"https://openalex.org/I1316902750","display_name":"Cleveland Clinic","ror":"https://ror.org/03xjacd83","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I1316902750"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Seth Rotz","raw_affiliation_strings":["Cleveland Clinic, Cleveland, Ohio"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Cleveland Clinic, Cleveland, Ohio","institution_ids":["https://openalex.org/I1316902750"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5070884470","display_name":"Joel Ofori","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]},{"id":"https://openalex.org/I4210146983","display_name":"Children's Healthcare of Atlanta","ror":"https://ror.org/050fhx250","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I4210146983"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Joel Ofori","raw_affiliation_strings":["Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia","institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5029066705","display_name":"Erin L. Frost","orcid":"https://orcid.org/0009-0006-8292-6123","observed_orcids":["https://orcid.org/0009-0006-8292-6123"]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]},{"id":"https://openalex.org/I4210146983","display_name":"Children's Healthcare of Atlanta","ror":"https://ror.org/050fhx250","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I4210146983"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Erin Frost","raw_affiliation_strings":["Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia","institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5134547478","display_name":"Jeremy Orbodo","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]},{"id":"https://openalex.org/I4210146983","display_name":"Children's Healthcare of Atlanta","ror":"https://ror.org/050fhx250","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I4210146983"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Jeremy Orbodo","raw_affiliation_strings":["Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia","institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5079820341","display_name":"Kathleen Spencer","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]},{"id":"https://openalex.org/I4210146983","display_name":"Children's Healthcare of Atlanta","ror":"https://ror.org/050fhx250","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I4210146983"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Kathleen Spencer","raw_affiliation_strings":["Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia","institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5070276405","display_name":"Ellen Kenney","orcid":"https://orcid.org/0009-0004-2723-2570","observed_orcids":["https://orcid.org/0009-0004-2723-2570"]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]},{"id":"https://openalex.org/I4210146983","display_name":"Children's Healthcare of Atlanta","ror":"https://ror.org/050fhx250","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I4210146983"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Ellen Kenney","raw_affiliation_strings":["Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia"],"raw_orcid":"https://orcid.org/0009-0004-2723-2570","affiliations":[{"raw_affiliation_string":"Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia","institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5063350418","display_name":"Satheesh Chonat","orcid":"https://orcid.org/0000-0002-5909-0800","observed_orcids":["https://orcid.org/0000-0002-5909-0800"]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]},{"id":"https://openalex.org/I4210146983","display_name":"Children's Healthcare of Atlanta","ror":"https://ror.org/050fhx250","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I4210146983"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Satheesh Chonat","raw_affiliation_strings":["Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia","institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5080975445","display_name":"Joseph H. Chewning","orcid":"https://orcid.org/0000-0001-5554-5890","observed_orcids":["https://orcid.org/0000-0001-5554-5890"]},"institutions":[{"id":"https://openalex.org/I320755355","display_name":"Children's of Alabama","ror":"https://ror.org/053bp9m60","country_code":"US","type":"funder","lineage":["https://openalex.org/I320755355"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Joseph Chewning","raw_affiliation_strings":["Children's of Alabama, Birmingham, Alabama"],"raw_orcid":"https://orcid.org/0000-0001-5554-5890","affiliations":[{"raw_affiliation_string":"Children's of Alabama, Birmingham, Alabama","institution_ids":["https://openalex.org/I320755355"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5061885926","display_name":"Caitlin Moore","orcid":"https://orcid.org/0009-0004-5767-4396","observed_orcids":["https://orcid.org/0009-0004-5767-4396"]},"institutions":[{"id":"https://openalex.org/I320755355","display_name":"Children's of Alabama","ror":"https://ror.org/053bp9m60","country_code":"US","type":"funder","lineage":["https://openalex.org/I320755355"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Caitlin Moore","raw_affiliation_strings":["Children's of Alabama, Birmingham, Alabama"],"raw_orcid":"https://orcid.org/0009-0004-5767-4396","affiliations":[{"raw_affiliation_string":"Children's of Alabama, Birmingham, Alabama","institution_ids":["https://openalex.org/I320755355"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5047494233","display_name":"Adrianna Lynn Westbrook","orcid":"https://orcid.org/0000-0001-9309-6205","observed_orcids":["https://orcid.org/0000-0001-9309-6205"]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Adrianna Westbrook","raw_affiliation_strings":["Pediatric Biostatistics Core, Department of Pediatrics, Emory University, Atlanta, Georgia"],"raw_orcid":"https://orcid.org/0000-0001-9309-6205","affiliations":[{"raw_affiliation_string":"Pediatric Biostatistics Core, Department of Pediatrics, Emory University, Atlanta, Georgia","institution_ids":["https://openalex.org/I150468666"]}]},{"author_position":"last","author":{"id":"https://openalex.org/A5125624851","display_name":"Kirsten M. Williams","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I150468666","display_name":"Emory University","ror":"https://ror.org/03czfpz43","country_code":"US","type":"education","lineage":["https://openalex.org/I150468666"]},{"id":"https://openalex.org/I4210146983","display_name":"Children's Healthcare of Atlanta","ror":"https://ror.org/050fhx250","country_code":"US","type":"healthcare","lineage":["https://openalex.org/I4210146983"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Kirsten M. Williams","raw_affiliation_strings":["Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Children's Healthcare of Atlanta, Aflac Cancer and Blood Disorders Center, Emory University, Atlanta, Georgia","institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"]}]}],"institutions":[],"countries_distinct_count":1,"institutions_distinct_count":10,"corresponding_author_ids":["https://openalex.org/A5046929879"],"corresponding_institution_ids":["https://openalex.org/I150468666","https://openalex.org/I4210146983"],"apc_list":{"value":3650,"currency":"USD","value_usd":3650},"apc_paid":null,"fwci":5.2801,"has_fulltext":false,"cited_by_count":2,"citation_normalized_percentile":{"value":0.9517681,"is_in_top_1_percent":false,"is_in_top_10_percent":true},"cited_by_percentile_year":{"min":96,"max":97},"biblio":{"volume":"32","issue":"7","first_page":"887.e1","last_page":"887.e16"},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T10993","display_name":"Complement system in diseases","score":1.0,"subfield":{"id":"https://openalex.org/subfields/2403","display_name":"Immunology"},"field":{"id":"https://openalex.org/fields/24","display_name":"Immunology and Microbiology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},"topics":[{"id":"https://openalex.org/T10993","display_name":"Complement system in diseases","score":1.0,"subfield":{"id":"https://openalex.org/subfields/2403","display_name":"Immunology"},"field":{"id":"https://openalex.org/fields/24","display_name":"Immunology and Microbiology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},{"id":"https://openalex.org/T10345","display_name":"Hematopoietic Stem Cell Transplantation","score":0.0,"subfield":{"id":"https://openalex.org/subfields/2720","display_name":"Hematology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T10373","display_name":"Renal Transplantation Outcomes and Treatments","score":0.0,"subfield":{"id":"https://openalex.org/subfields/2747","display_name":"Transplantation"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/eculizumab","display_name":"eculizumab","score":0.9470000267028809},{"id":"https://openalex.org/keywords/transplant-associated-thrombotic-microangiopathy","display_name":"transplant-associated thrombotic microangiopathy","score":0.9539999961853027},{"id":"https://openalex.org/keywords/pediatric-hematopoietic-stem-cell-transplantation","display_name":"pediatric hematopoietic stem cell transplantation","score":0.9309999942779541},{"id":"https://openalex.org/keywords/complement-c5-inhibition","display_name":"complement C5 inhibition","score":0.7559999823570251},{"id":"https://openalex.org/keywords/treatment-response-rate","display_name":"treatment response rate","score":0.5569999814033508},{"id":"https://openalex.org/keywords/treatment-related-mortality","display_name":"non-relapse mortality","score":0.8479999899864197},{"id":"https://openalex.org/keywords/acute-graft-versus-host-disease","display_name":"acute graft-versus-host disease","score":0.7710000276565552},{"id":"https://openalex.org/keywords/multiple-organ-failure","display_name":"multiple organ failure","score":0.7390000224113464},{"id":"https://openalex.org/keywords/allogeneic-vs-autologous-transplantation","display_name":"allogeneic vs autologous transplantation","score":0.796999990940094},{"id":"https://openalex.org/keywords/off-label-therapy","display_name":"off-label therapy","score":0.5329999923706055},{"id":"https://openalex.org/keywords/real-world-outcomes","display_name":"real-world outcomes","score":0.6370000243186951}],"concepts":[{"id":"https://openalex.org/C71924100","wikidata":"https://www.wikidata.org/wiki/Q11190","display_name":"Medicine","level":0,"score":0.8755999803543091},{"id":"https://openalex.org/C2777991916","wikidata":"https://www.wikidata.org/wiki/Q421617","display_name":"Eculizumab","level":4,"score":0.8504999876022339},{"id":"https://openalex.org/C126322002","wikidata":"https://www.wikidata.org/wiki/Q11180","display_name":"Internal medicine","level":1,"score":0.5694000124931335},{"id":"https://openalex.org/C143998085","wikidata":"https://www.wikidata.org/wiki/Q162555","display_name":"Oncology","level":1,"score":0.43950000405311584},{"id":"https://openalex.org/C2993713153","wikidata":"https://www.wikidata.org/wiki/Q211709","display_name":"Hematopoietic cell","level":4,"score":0.3582000136375427},{"id":"https://openalex.org/C177713679","wikidata":"https://www.wikidata.org/wiki/Q679690","display_name":"Intensive care medicine","level":1,"score":0.3352000117301941},{"id":"https://openalex.org/C535046627","wikidata":"https://www.wikidata.org/wiki/Q30612","display_name":"Clinical trial","level":2,"score":0.3280999958515167},{"id":"https://openalex.org/C2779473830","wikidata":"https://www.wikidata.org/wiki/Q1540899","display_name":"MEDLINE","level":2,"score":0.3125},{"id":"https://openalex.org/C2776915898","wikidata":"https://www.wikidata.org/wiki/Q1235195","display_name":"Romiplostim","level":5,"score":0.30320000648498535},{"id":"https://openalex.org/C2777408962","wikidata":"https://www.wikidata.org/wiki/Q1128050","display_name":"Hematopoietic stem cell transplantation","level":3,"score":0.28119999170303345},{"id":"https://openalex.org/C3020493868","wikidata":"https://www.wikidata.org/wiki/Q55631277","display_name":"Real world data","level":2,"score":0.26840001344680786},{"id":"https://openalex.org/C12174686","wikidata":"https://www.wikidata.org/wiki/Q1058438","display_name":"Risk assessment","level":2,"score":0.257999986410141}],"mesh":[{"descriptor_ui":"D000293","descriptor_name":"Adolescent","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D002648","descriptor_name":"Child","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D002675","descriptor_name":"Child, Preschool","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D005260","descriptor_name":"Female","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D006801","descriptor_name":"Humans","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D007223","descriptor_name":"Infant","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D008297","descriptor_name":"Male","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D012189","descriptor_name":"Retrospective Studies","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D013997","descriptor_name":"Time Factors","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D016896","descriptor_name":"Treatment Outcome","qualifier_ui":null,"qualifier_name":null,"is_major_topic":false},{"descriptor_ui":"D018380","descriptor_name":"Hematopoietic Stem Cell Transplantation","qualifier_ui":"Q000009","qualifier_name":"adverse effects","is_major_topic":true},{"descriptor_ui":"D051056","descriptor_name":"Complement Inactivating Agents","qualifier_ui":"Q000627","qualifier_name":"therapeutic use","is_major_topic":true},{"descriptor_ui":"D057049","descriptor_name":"Thrombotic Microangiopathies","qualifier_ui":"Q000188","qualifier_name":"drug therapy","is_major_topic":true},{"descriptor_ui":"D057049","descriptor_name":"Thrombotic Microangiopathies","qualifier_ui":"Q000209","qualifier_name":"etiology","is_major_topic":true},{"descriptor_ui":"D061067","descriptor_name":"Antibodies, Monoclonal, Humanized","qualifier_ui":"Q000494","qualifier_name":"pharmacology","is_major_topic":true},{"descriptor_ui":"D061067","descriptor_name":"Antibodies, Monoclonal, Humanized","qualifier_ui":"Q000627","qualifier_name":"therapeutic use","is_major_topic":true}],"locations_count":2,"locations":[{"id":"doi:10.1016/j.jtct.2026.04.026","doi":"https://doi.org/10.1016/j.jtct.2026.04.026","is_oa":false,"landing_page_url":"https://doi.org/10.1016/j.jtct.2026.04.026","pdf_url":null,"source":{"id":"https://openalex.org/S59987174","display_name":"Transplantation and Cellular Therapy","issn_l":"1083-8791","issn":["1083-8791","1523-6536","2666-6367"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","poland-100","poland-20","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Transplantation and Cellular Therapy","raw_type":"journal-article"},{"id":"pmid:42035874","doi":null,"is_oa":false,"landing_page_url":"https://pubmed.ncbi.nlm.nih.gov/42035874","pdf_url":null,"source":{"id":"https://openalex.org/S4306525036","display_name":"PubMed","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/I1299303238","host_organization_name":"National Institutes of Health","host_organization_lineage":["https://openalex.org/I1299303238"],"host_organization_lineage_names":[],"type":"repository"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Transplantation and cellular therapy","raw_type":"Journal Article"}],"best_oa_location":null,"sustainable_development_goals":[{"id":"https://metadata.un.org/sdg/3","score":1.0,"display_name":"Good health and well-being"}],"study_designs":[{"id":"https://openalex.org/study-designs/observational-study","display_name":"Observational Study"}],"awards":[{"id":"https://openalex.org/G9000901456","display_name":"Research Training in Childhood Cancer","funder_award_id":"T32CA128583","funder_id":"https://openalex.org/F4320337351","funder_display_name":"National Cancer Institute"}],"funders":[{"id":"https://openalex.org/F4320337351","display_name":"National Cancer Institute","ror":"https://ror.org/040gcmg81"}],"has_content":{"pdf":false,"grobid_xml":false},"content_urls":null,"referenced_works_count":41,"referenced_works":["https://openalex.org/W1972848999","https://openalex.org/W1979637902","https://openalex.org/W1985894108","https://openalex.org/W1993215990","https://openalex.org/W2091375248","https://openalex.org/W2117803220","https://openalex.org/W2141010787","https://openalex.org/W2326205797","https://openalex.org/W2335781036","https://openalex.org/W2579476173","https://openalex.org/W2621741324","https://openalex.org/W2717271878","https://openalex.org/W2736218182","https://openalex.org/W2753099642","https://openalex.org/W2792985650","https://openalex.org/W2793137791","https://openalex.org/W2799295920","https://openalex.org/W2809099134","https://openalex.org/W2887792780","https://openalex.org/W2898432878","https://openalex.org/W2917105156","https://openalex.org/W2923881376","https://openalex.org/W2953407874","https://openalex.org/W2978460082","https://openalex.org/W3010121256","https://openalex.org/W3012952745","https://openalex.org/W3033416765","https://openalex.org/W3113832250","https://openalex.org/W3213074348","https://openalex.org/W4224264092","https://openalex.org/W4225114034","https://openalex.org/W4308257579","https://openalex.org/W4309963096","https://openalex.org/W4313368125","https://openalex.org/W4388571905","https://openalex.org/W4390322684","https://openalex.org/W4390499277","https://openalex.org/W4393237260","https://openalex.org/W4399999867","https://openalex.org/W4409907966","https://openalex.org/W4411220087"],"related_works":["https://openalex.org/W4407977533","https://openalex.org/W4308257579","https://openalex.org/W4393237260","https://openalex.org/W4391617444","https://openalex.org/W7127340753","https://openalex.org/W3213074348","https://openalex.org/W2809099134","https://openalex.org/W4407975333","https://openalex.org/W2908566839","https://openalex.org/W7204715866"],"abstract_inverted_index":null,"counts_by_year":[{"year":2026,"cited_by_count":2}],"updated_date":"2026-10-31T12:09:11.096373","created_date":"2026-04-25T00:00:00"}
