{"id":"https://openalex.org/W7136229300","doi":"https://doi.org/10.6084/m9.figshare.4422818","title":"Additional file 1: of rAAV-compatible MiniPromoters for restricted expression in the brain and eye","display_name":"Additional file 1: of rAAV-compatible MiniPromoters for restricted expression in the brain and eye","publication_year":2016,"publication_date":"2016-01-01","ids":{"openalex":"https://openalex.org/W7136229300","doi":"https://doi.org/10.6084/m9.figshare.4422818"},"language":"en","primary_location":{"id":"doi:10.6084/m9.figshare.4422818","doi":"https://doi.org/10.6084/m9.figshare.4422818","is_oa":true,"landing_page_url":"https://doi.org/10.6084/m9.figshare.4422818","pdf_url":null,"source":{"id":"https://openalex.org/S4377196282","display_name":"Figshare","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/I4210132348","host_organization_name":"Figshare (United Kingdom)","host_organization_lineage":["https://openalex.org/I4210132348"],"host_organization_lineage_names":[],"type":"repository"},"license":"cc-by","license_id":"https://openalex.org/licenses/cc-by","version":null,"is_accepted":false,"is_published":false,"raw_source_name":null,"raw_type":"JournalArticle"},"volume":null,"type":"article","indexed_in":["datacite"],"open_access":{"is_oa":true,"oa_status":"green","oa_url":"https://doi.org/10.6084/m9.figshare.4422818","any_repository_has_fulltext":true},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5023491070","display_name":"Charles N. de Leeuw","orcid":"https://orcid.org/0000-0001-9413-2095","observed_orcids":["https://orcid.org/0000-0001-9413-2095"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"de Leeuw, Charles","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5030802637","display_name":"Andrea J. Korecki","orcid":"https://orcid.org/0000-0001-6532-0695","observed_orcids":["https://orcid.org/0000-0001-6532-0695"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Korecki, Andrea","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5034280337","display_name":"Garrett E. Berry","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Berry, Garrett","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5069973478","display_name":"Jack W. Hickmott","orcid":"https://orcid.org/0000-0003-3764-1138","observed_orcids":["https://orcid.org/0000-0003-3764-1138"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Hickmott, Jack","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5112472836","display_name":"Siu Ling Lam","orcid":"https://orcid.org/0009-0003-7583-0789","observed_orcids":["https://orcid.org/0009-0003-7583-0789"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Lam, Siu","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5031038532","display_name":"Tess C. Lengyell","orcid":"https://orcid.org/0000-0001-6292-0724","observed_orcids":["https://orcid.org/0000-0001-6292-0724"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Lengyell, Tess","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5044095938","display_name":"Russell J. Bonaguro","orcid":"https://orcid.org/0000-0003-2581-6252","observed_orcids":["https://orcid.org/0000-0003-2581-6252"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Bonaguro, Russell","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5031891255","display_name":"Lisa Borretta","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Borretta, Lisa","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5077687405","display_name":"Vikramjit S. Chopra","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Chopra, Vikramjit","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5085981678","display_name":"Alice Chou","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Chou, Alice","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5129575032","display_name":"Cletus D\u2019Souza","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"D\u00e2\u0080\u0099Souza, Cletus","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5040056811","display_name":"Olga Kaspieva","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Kaspieva, Olga","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5129615386","display_name":"St\u0102\u0160phanie Laprise","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Laprise, St\u0102\u0160phanie","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5057064334","display_name":"Simone McInerny","orcid":"https://orcid.org/0000-0002-5048-1549","observed_orcids":["https://orcid.org/0000-0002-5048-1549"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"McInerny, Simone","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5000462169","display_name":"\u00c9lodie Portales-Casamar","orcid":"https://orcid.org/0000-0002-9998-7858","observed_orcids":["https://orcid.org/0000-0002-9998-7858"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Portales-Casamar, Elodie","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5027171577","display_name":"Magdalena I. Swanson-Newman","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Swanson-Newman, Magdalena","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5048745172","display_name":"Kaelan Wong","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Wong, Kaelan","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5111713976","display_name":"George Yang","orcid":"https://orcid.org/0009-0004-1778-2755","observed_orcids":["https://orcid.org/0009-0004-1778-2755"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Yang, George","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5129482389","display_name":"Michelle Zhou","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Zhou, Michelle","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5129636225","display_name":"Steven Jones","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Jones, Steven","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5065733774","display_name":"Robert A. Holt","orcid":"https://orcid.org/0000-0002-7259-1247","observed_orcids":["https://orcid.org/0000-0002-7259-1247","https://orcid.org/0009-0002-1565-5205"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Holt, Robert","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5019219512","display_name":"Aravind Asokan","orcid":"https://orcid.org/0000-0001-5563-4877","observed_orcids":["https://orcid.org/0000-0001-5563-4877"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Asokan, Aravind","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5016295259","display_name":"Dan Goldowitz","orcid":"https://orcid.org/0000-0003-4756-4017","observed_orcids":["https://orcid.org/0000-0003-4756-4017"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Goldowitz, Daniel","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5026664289","display_name":"Wyeth W. Wasserman","orcid":"https://orcid.org/0000-0001-6098-6412","observed_orcids":["https://orcid.org/0000-0001-6098-6412"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Wasserman, Wyeth","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"last","author":{"id":"https://openalex.org/A5065488747","display_name":"Elizabeth M. Simpson","orcid":"https://orcid.org/0000-0002-0654-4303","observed_orcids":["https://orcid.org/0000-0002-0654-4303"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Simpson, Elizabeth","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]}],"institutions":[],"countries_distinct_count":0,"institutions_distinct_count":0,"corresponding_author_ids":[],"corresponding_institution_ids":[],"apc_list":null,"apc_paid":null,"fwci":0.0,"has_fulltext":false,"cited_by_count":0,"citation_normalized_percentile":{"value":0.62721497,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":null,"biblio":{"volume":null,"issue":null,"first_page":null,"last_page":null},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T10613","display_name":"Virus-based gene therapy research","score":0.9883000254631042,"subfield":{"id":"https://openalex.org/subfields/1311","display_name":"Genetics"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},"topics":[{"id":"https://openalex.org/T10613","display_name":"Virus-based gene therapy research","score":0.9883000254631042,"subfield":{"id":"https://openalex.org/subfields/1311","display_name":"Genetics"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},{"id":"https://openalex.org/T10725","display_name":"RNA Interference and Gene Delivery","score":0.005499999970197678,"subfield":{"id":"https://openalex.org/subfields/1312","display_name":"Molecular Biology"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},{"id":"https://openalex.org/T11872","display_name":"Barrier Structure and Function Studies","score":0.0010999999940395355,"subfield":{"id":"https://openalex.org/subfields/2808","display_name":"Neurology"},"field":{"id":"https://openalex.org/fields/28","display_name":"Neuroscience"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/recombinant-adeno-associated-virus","display_name":"recombinant adeno-associated virus","score":0.8730000257492065},{"id":"https://openalex.org/keywords/raav-vectors","display_name":"rAAV vectors","score":0.7039999961853027},{"id":"https://openalex.org/keywords/brain-expression","display_name":"brain expression","score":0.6890000104904175},{"id":"https://openalex.org/keywords/eye-expression","display_name":"eye expression","score":0.8510000109672546},{"id":"https://openalex.org/keywords/gene-delivery","display_name":"gene delivery","score":0.5590000152587891}],"concepts":[{"id":"https://openalex.org/C90559484","wikidata":"https://www.wikidata.org/wiki/Q778379","display_name":"Expression (computer science)","level":2,"score":0.5720999836921692},{"id":"https://openalex.org/C41008148","wikidata":"https://www.wikidata.org/wiki/Q21198","display_name":"Computer science","level":0,"score":0.4577000141143799},{"id":"https://openalex.org/C86803240","wikidata":"https://www.wikidata.org/wiki/Q420","display_name":"Biology","level":0,"score":0.4072999954223633},{"id":"https://openalex.org/C154945302","wikidata":"https://www.wikidata.org/wiki/Q11660","display_name":"Artificial intelligence","level":1,"score":0.31540000438690186},{"id":"https://openalex.org/C54355233","wikidata":"https://www.wikidata.org/wiki/Q7162","display_name":"Genetics","level":1,"score":0.30730000138282776},{"id":"https://openalex.org/C150194340","wikidata":"https://www.wikidata.org/wiki/Q26972","display_name":"Gene expression","level":3,"score":0.2992999851703644},{"id":"https://openalex.org/C70721500","wikidata":"https://www.wikidata.org/wiki/Q177005","display_name":"Computational biology","level":1,"score":0.27399998903274536},{"id":"https://openalex.org/C2776401178","wikidata":"https://www.wikidata.org/wiki/Q12050496","display_name":"Feature (linguistics)","level":2,"score":0.26759999990463257},{"id":"https://openalex.org/C169760540","wikidata":"https://www.wikidata.org/wiki/Q207011","display_name":"Neuroscience","level":1,"score":0.24289999902248383},{"id":"https://openalex.org/C501734568","wikidata":"https://www.wikidata.org/wiki/Q42918","display_name":"Mutation","level":3,"score":0.23080000281333923}],"mesh":[],"locations_count":2,"locations":[{"id":"doi:10.6084/m9.figshare.4422818","doi":"https://doi.org/10.6084/m9.figshare.4422818","is_oa":true,"landing_page_url":"https://doi.org/10.6084/m9.figshare.4422818","pdf_url":null,"source":{"id":"https://openalex.org/S4377196282","display_name":"Figshare","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/I4210132348","host_organization_name":"Figshare (United Kingdom)","host_organization_lineage":["https://openalex.org/I4210132348"],"host_organization_lineage_names":[],"type":"repository"},"license":"cc-by","license_id":"https://openalex.org/licenses/cc-by","version":null,"is_accepted":false,"is_published":false,"raw_source_name":null,"raw_type":"JournalArticle"},{"id":"doi:10.6084/m9.figshare.4422818.v1","doi":"https://doi.org/10.6084/m9.figshare.4422818.v1","is_oa":true,"landing_page_url":"https://doi.org/10.6084/m9.figshare.4422818.v1","pdf_url":null,"source":{"id":"https://openalex.org/S4377196282","display_name":"Figshare","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/I4210132348","host_organization_name":"Figshare (United Kingdom)","host_organization_lineage":["https://openalex.org/I4210132348"],"host_organization_lineage_names":[],"type":"repository"},"license":"cc-by","license_id":"https://openalex.org/licenses/cc-by","version":null,"is_accepted":false,"is_published":false,"raw_source_name":null,"raw_type":"JournalArticle"}],"best_oa_location":{"id":"doi:10.6084/m9.figshare.4422818","doi":"https://doi.org/10.6084/m9.figshare.4422818","is_oa":true,"landing_page_url":"https://doi.org/10.6084/m9.figshare.4422818","pdf_url":null,"source":{"id":"https://openalex.org/S4377196282","display_name":"Figshare","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/I4210132348","host_organization_name":"Figshare (United Kingdom)","host_organization_lineage":["https://openalex.org/I4210132348"],"host_organization_lineage_names":[],"type":"repository"},"license":"cc-by","license_id":"https://openalex.org/licenses/cc-by","version":null,"is_accepted":false,"is_published":false,"raw_source_name":null,"raw_type":"JournalArticle"},"sustainable_development_goals":[],"study_designs":[],"awards":[],"funders":[],"has_content":{"pdf":false,"grobid_xml":false},"content_urls":null,"referenced_works_count":0,"referenced_works":[],"related_works":["https://openalex.org/W2365630593","https://openalex.org/W4241479699","https://openalex.org/W4389903477","https://openalex.org/W2566994691","https://openalex.org/W7126103003","https://openalex.org/W1988340904","https://openalex.org/W2313914167","https://openalex.org/W1133208563","https://openalex.org/W2518556646","https://openalex.org/W4229827965"],"abstract_inverted_index":{"Supplementary":[0],"Figures":[1],"1":[2],"-":[3],"6.":[4],"(PDF":[5],"10":[6],"kb)":[7]},"counts_by_year":[],"updated_date":"2026-10-30T12:39:25.321706","created_date":"2026-03-17T00:00:00"}
