{"id":"https://openalex.org/W4310124540","doi":"https://doi.org/10.1182/blood-2022-169086","title":"Current Use of Androgens in Bone Marrow Failure Disorders: A Report from the Severe Aplastic Anemia Working Party (SAAWP) of the European Society of Blood and Marrow Transplantation (EBMT)","display_name":"Current Use of Androgens in Bone Marrow Failure Disorders: A Report from the Severe Aplastic Anemia Working Party (SAAWP) of the European Society of Blood and Marrow Transplantation (EBMT)","publication_year":2022,"publication_date":"2022-11-15","ids":{"openalex":"https://openalex.org/W4310124540","doi":"https://doi.org/10.1182/blood-2022-169086"},"language":"en","primary_location":{"id":"doi:10.1182/blood-2022-169086","doi":"https://doi.org/10.1182/blood-2022-169086","is_oa":false,"landing_page_url":"https://doi.org/10.1182/blood-2022-169086","pdf_url":null,"source":{"id":"https://openalex.org/S200071133","display_name":"Blood","issn_l":"0006-4971","issn":["0006-4971","1528-0020"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-a","doyens","jufo-3","ki-jl-3","medline","norway-2","poland-200","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Blood","raw_type":"journal-article"},"volume":null,"type":"article","indexed_in":["crossref"],"open_access":{"is_oa":false,"oa_status":"closed","oa_url":null,"any_repository_has_fulltext":false},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5066332957","display_name":"Simona Pagliuca","orcid":"https://orcid.org/0000-0003-4688-2478","observed_orcids":["https://orcid.org/0000-0003-4688-2478"]},"institutions":[{"id":"https://openalex.org/I1294671590","display_name":"Centre National de la Recherche Scientifique","ror":"https://ror.org/02feahw73","country_code":"FR","type":"government","lineage":["https://openalex.org/I1294671590"]},{"id":"https://openalex.org/I4210100260","display_name":"Centre Hospitalier R\u00e9gional et Universitaire de Nancy","ror":"https://ror.org/016ncsr12","country_code":"FR","type":"healthcare","lineage":["https://openalex.org/I4210100260"]},{"id":"https://openalex.org/I4210152866","display_name":"Ing\u00e9nierie Mol\u00e9culaire, Cellulaire et Physiopathologie","ror":"https://ror.org/04yc2e502","country_code":"FR","type":"facility","lineage":["https://openalex.org/I1294671590","https://openalex.org/I4210095849","https://openalex.org/I4210100260","https://openalex.org/I4210152866","https://openalex.org/I90183372"]},{"id":"https://openalex.org/I90183372","display_name":"Universit\u00e9 de Lorraine","ror":"https://ror.org/04vfs2w97","country_code":"FR","type":"education","lineage":["https://openalex.org/I90183372"]}],"countries":["FR"],"is_corresponding":false,"raw_author_name":"Simona Pagliuca","raw_affiliation_strings":["1Department of Clinical Hematology, CHRU Nancy, Vand\u0153uvre-l\u00e8s-Nancy, France","2CNRS UMR 7365 IMoPa, Biop\u00f4le de l'Universit\u00e9 de Lorraine, Vand\u0153uvre-l\u00e8s-Nancy, France"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"1Department of Clinical Hematology, CHRU Nancy, Vand\u0153uvre-l\u00e8s-Nancy, France","institution_ids":["https://openalex.org/I4210100260"]},{"raw_affiliation_string":"2CNRS UMR 7365 IMoPa, Biop\u00f4le de l'Universit\u00e9 de Lorraine, Vand\u0153uvre-l\u00e8s-Nancy, France","institution_ids":["https://openalex.org/I1294671590","https://openalex.org/I4210152866","https://openalex.org/I90183372"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5045018770","display_name":"Austin Gladston Kulasekararaj","orcid":"https://orcid.org/0000-0003-3180-3570","observed_orcids":["https://orcid.org/0000-0003-3180-3570"]},"institutions":[{"id":"https://openalex.org/I34931013","display_name":"National Institute for Health and Care Research","ror":"https://ror.org/0187kwz08","country_code":"GB","type":"government","lineage":["https://openalex.org/I34931013"]},{"id":"https://openalex.org/I4210111135","display_name":"King's College Hospital NHS Foundation Trust","ror":"https://ror.org/01n0k5m85","country_code":"GB","type":"healthcare","lineage":["https://openalex.org/I4210111135"]},{"id":"https://openalex.org/I4210153400","display_name":"King's College Hospital","ror":"https://ror.org/044nptt90","country_code":"GB","type":"healthcare","lineage":["https://openalex.org/I4210111135","https://openalex.org/I4210153400"]}],"countries":["GB"],"is_corresponding":false,"raw_author_name":"Austin Kulasekararaj","raw_affiliation_strings":["3King's College Hospital, National Institute for Health and Care Research/Wellcome King's Clinical Research Facility, London, United Kingdom"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"3King's College Hospital, National Institute for Health and Care Research/Wellcome King's Clinical Research Facility, London, United Kingdom","institution_ids":["https://openalex.org/I34931013","https://openalex.org/I4210111135","https://openalex.org/I4210153400"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5033587177","display_name":"Dirk\u2010Jan Eikema","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I4210099689","display_name":"European Society for Blood and Marrow Transplantation","ror":"https://ror.org/014wq8057","country_code":"NL","type":"nonprofit","lineage":["https://openalex.org/I4210099689"]}],"countries":["NL"],"is_corresponding":false,"raw_author_name":"Dirk-Jan Eikema","raw_affiliation_strings":["4EBMT Statistical Unit, Leiden, Netherlands"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"4EBMT Statistical Unit, Leiden, Netherlands","institution_ids":["https://openalex.org/I4210099689"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5075777920","display_name":"Brian Piepenbroek","orcid":"https://orcid.org/0009-0006-5990-2211","observed_orcids":["https://orcid.org/0009-0006-5990-2211"]},"institutions":[{"id":"https://openalex.org/I4210099689","display_name":"European Society for Blood and Marrow Transplantation","ror":"https://ror.org/014wq8057","country_code":"NL","type":"nonprofit","lineage":["https://openalex.org/I4210099689"]}],"countries":["NL"],"is_corresponding":false,"raw_author_name":"Brian Piepenbroek","raw_affiliation_strings":["5EBMT Leiden Study Unit, Leiden, Netherlands"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"5EBMT Leiden Study Unit, Leiden, Netherlands","institution_ids":["https://openalex.org/I4210099689"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5044676471","display_name":"Raheel Iftikhar","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Raheel Iftikhar","raw_affiliation_strings":["6Armed Forces Bone MarrowTransplant Centre, Rawalpindi, Pakistan"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"6Armed Forces Bone MarrowTransplant Centre, Rawalpindi, Pakistan","institution_ids":[]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5108491975","display_name":"Tariq Mahmood Satti","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Tariq Mahmood Satti","raw_affiliation_strings":["6Armed Forces Bone MarrowTransplant Centre, Rawalpindi, Pakistan"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"6Armed Forces Bone MarrowTransplant Centre, Rawalpindi, Pakistan","institution_ids":[]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5031046212","display_name":"Morag Griffin","orcid":"https://orcid.org/0000-0002-4287-0595","observed_orcids":["https://orcid.org/0000-0002-4287-0595"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Morag Griffin","raw_affiliation_strings":["7St James's University Hospital, Sheffield, United Kingdom"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"7St James's University Hospital, Sheffield, United Kingdom","institution_ids":[]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5039467121","display_name":"Marica Laurino","orcid":"https://orcid.org/0000-0003-3719-1085","observed_orcids":["https://orcid.org/0000-0003-3719-1085"]},"institutions":[{"id":"https://openalex.org/I4210146472","display_name":"Ospedale Policlinico San Martino","ror":"https://ror.org/04d7es448","country_code":"IT","type":"healthcare","lineage":["https://openalex.org/I4210146472","https://openalex.org/I4210153126","https://openalex.org/I4405264730"]}],"countries":["IT"],"is_corresponding":false,"raw_author_name":"Marica Laurino","raw_affiliation_strings":["8UO ematologia e terapie cellulari, IRCCS Ospedale Policlinico San martino, Genova, Italy"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"8UO ematologia e terapie cellulari, IRCCS Ospedale Policlinico San martino, Genova, Italy","institution_ids":["https://openalex.org/I4210146472"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5058502232","display_name":"Alphan K\u00fcpesiz","orcid":"https://orcid.org/0000-0001-8827-5567","observed_orcids":["https://orcid.org/0000-0001-8827-5567"]},"institutions":[{"id":"https://openalex.org/I197907453","display_name":"Akdeniz University","ror":"https://ror.org/01m59r132","country_code":"TR","type":"education","lineage":["https://openalex.org/I197907453"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"O. Alphan Kupesiz","raw_affiliation_strings":["9Hematology Department, Akdeniz University Medical School, Antalya, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"9Hematology Department, Akdeniz University Medical School, Antalya, Turkey","institution_ids":["https://openalex.org/I197907453"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5084698361","display_name":"Yives Bertrand","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I100532134","display_name":"Lyon 1 Universit\u00e9","ror":"https://ror.org/029brtt94","country_code":"FR","type":"education","lineage":["https://openalex.org/I100532134","https://openalex.org/I203339264"]}],"countries":["FR"],"is_corresponding":false,"raw_author_name":"Yives Bertrand","raw_affiliation_strings":["10Institute of Pediatric Hematology and Oncology, Civil Hospital of Lyon - Claude Bernard University, Lyon, France"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"10Institute of Pediatric Hematology and Oncology, Civil Hospital of Lyon - Claude Bernard University, Lyon, France","institution_ids":["https://openalex.org/I100532134"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5076368199","display_name":"Bruno Fattizzo","orcid":"https://orcid.org/0000-0003-0857-8379","observed_orcids":["https://orcid.org/0000-0003-0857-8379"]},"institutions":[{"id":"https://openalex.org/I2803066834","display_name":"Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico","ror":"https://ror.org/016zn0y21","country_code":"IT","type":"healthcare","lineage":["https://openalex.org/I189158943","https://openalex.org/I2803066834","https://openalex.org/I4210153126"]}],"countries":["IT"],"is_corresponding":false,"raw_author_name":"Bruno Fattizzo","raw_affiliation_strings":["11Dipartimento di Oncologia e Emato-Oncologia, Fondazione IRCCS Ca\u2019 Granda - Ospedale Maggiore Policlinico, Milano, Italy"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"11Dipartimento di Oncologia e Emato-Oncologia, Fondazione IRCCS Ca\u2019 Granda - Ospedale Maggiore Policlinico, Milano, Italy","institution_ids":["https://openalex.org/I2803066834"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5050987906","display_name":"Ibrahim Yakoub\u2010Agha","orcid":"https://orcid.org/0000-0003-4524-8782","observed_orcids":["https://orcid.org/0000-0003-4524-8782"]},"institutions":[{"id":"https://openalex.org/I154526488","display_name":"Inserm","ror":"https://ror.org/02vjkv261","country_code":"FR","type":"government","lineage":["https://openalex.org/I154526488"]},{"id":"https://openalex.org/I2279609970","display_name":"Universit\u00e9 de Lille","ror":"https://ror.org/02kzqn938","country_code":"FR","type":"education","lineage":["https://openalex.org/I2279609970"]},{"id":"https://openalex.org/I3018718406","display_name":"Centre Hospitalier Universitaire de Lille","ror":"https://ror.org/02ppyfa04","country_code":"FR","type":"healthcare","lineage":["https://openalex.org/I3018718406"]},{"id":"https://openalex.org/I4210128436","display_name":"Lille Inflammation Research International Center","ror":"https://ror.org/03c3m6m66","country_code":"FR","type":"facility","lineage":["https://openalex.org/I154526488","https://openalex.org/I2279609970","https://openalex.org/I3018718406","https://openalex.org/I4210093160","https://openalex.org/I4210128436","https://openalex.org/I4387152267"]},{"id":"https://openalex.org/I4387152267","display_name":"Institute for Translational Research in Inflammation","ror":"https://ror.org/03qy9z186","country_code":"FR","type":"facility","lineage":["https://openalex.org/I154526488","https://openalex.org/I2279609970","https://openalex.org/I3018718406","https://openalex.org/I4387152267"]}],"countries":["FR"],"is_corresponding":false,"raw_author_name":"Ibrahim Yakoub-Agha","raw_affiliation_strings":["12Centre Hospitalier Universitaire de Lille LIRIC, INSERM U1286, Universit\u00e9 de Lille, LILLE, France"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"12Centre Hospitalier Universitaire de Lille LIRIC, INSERM U1286, Universit\u00e9 de Lille, LILLE, France","institution_ids":["https://openalex.org/I154526488","https://openalex.org/I2279609970","https://openalex.org/I3018718406","https://openalex.org/I4210128436","https://openalex.org/I4387152267"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5083504452","display_name":"Mahmoud Deeb Aljurf","orcid":"https://orcid.org/0000-0003-3942-7370","observed_orcids":["https://orcid.org/0000-0003-3942-7370"]},"institutions":[{"id":"https://openalex.org/I2800965796","display_name":"King Faisal Specialist Hospital & Research Centre","ror":"https://ror.org/05n0wgt02","country_code":"SA","type":"healthcare","lineage":["https://openalex.org/I2800965796"]}],"countries":["SA"],"is_corresponding":false,"raw_author_name":"Mahmoud Aljurf","raw_affiliation_strings":["13Oncology Center, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"13Oncology Center, King Faisal Specialist Hospital and Research Center, Riyadh, Saudi Arabia","institution_ids":["https://openalex.org/I2800965796"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5102970561","display_name":"Paola Consuelo Corti","orcid":"https://orcid.org/0000-0002-4178-3633","observed_orcids":["https://orcid.org/0000-0002-4178-3633"]},"institutions":[{"id":"https://openalex.org/I66752286","display_name":"University of Milano-Bicocca","ror":"https://ror.org/01ynf4891","country_code":"IT","type":"education","lineage":["https://openalex.org/I66752286"]}],"countries":["IT"],"is_corresponding":false,"raw_author_name":"Paola Corti","raw_affiliation_strings":["14Pediatric Hemato-Oncolgy, Fondazione MBBM/ASST-Monza, University of Milano-Bicocca, Monza, Italy"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"14Pediatric Hemato-Oncolgy, Fondazione MBBM/ASST-Monza, University of Milano-Bicocca, Monza, Italy","institution_ids":["https://openalex.org/I66752286"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5034545586","display_name":"Erika Massaccesi","orcid":"https://orcid.org/0009-0006-4682-3426","observed_orcids":["https://orcid.org/0009-0006-4682-3426"]},"institutions":[{"id":"https://openalex.org/I2801463291","display_name":"Istituto Giannina Gaslini","ror":"https://ror.org/0424g0k78","country_code":"IT","type":"healthcare","lineage":["https://openalex.org/I2801463291","https://openalex.org/I4210153126"]}],"countries":["IT"],"is_corresponding":false,"raw_author_name":"Erika Massaccesi","raw_affiliation_strings":["15IRCSS Istituto Giannina Gaslini, Genoa, Italy"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"15IRCSS Istituto Giannina Gaslini, Genoa, Italy","institution_ids":["https://openalex.org/I2801463291"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5015832963","display_name":"Bruno Lioure","orcid":"https://orcid.org/0000-0003-0897-3416","observed_orcids":["https://orcid.org/0000-0003-0897-3416"]},"institutions":[{"id":"https://openalex.org/I4210145324","display_name":"H\u00f4pitaux Universitaires de Strasbourg","ror":"https://ror.org/04bckew43","country_code":"FR","type":"healthcare","lineage":["https://openalex.org/I4210145324"]}],"countries":["FR"],"is_corresponding":false,"raw_author_name":"Bruno Lioure","raw_affiliation_strings":["16Centre Hospitalier Universitaire de Strasbourg, Strasbourg, France"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"16Centre Hospitalier Universitaire de Strasbourg, Strasbourg, France","institution_ids":["https://openalex.org/I4210145324"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5057774263","display_name":"Marisa Calabuig","orcid":"https://orcid.org/0000-0002-3250-820X","observed_orcids":["https://orcid.org/0000-0002-3250-820X"]},"institutions":[{"id":"https://openalex.org/I4210094406","display_name":"Hospital Cl\u00ednico Universitario de Valencia","ror":"https://ror.org/00hpnj894","country_code":"ES","type":"healthcare","lineage":["https://openalex.org/I4210094406"]}],"countries":["ES"],"is_corresponding":false,"raw_author_name":"Marisa Calabuig","raw_affiliation_strings":["17Hospital Cl\u00ednico de Valencia, Valencia, Spain"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"17Hospital Cl\u00ednico de Valencia, Valencia, Spain","institution_ids":["https://openalex.org/I4210094406"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5087077867","display_name":"Matthias Klammer","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I165862685","display_name":"St George's, University of London","ror":"https://ror.org/040f08y74","country_code":"GB","type":"education","lineage":["https://openalex.org/I124357947","https://openalex.org/I165862685","https://openalex.org/I4401726869"]}],"countries":["GB"],"is_corresponding":false,"raw_author_name":"Matthias Klammer","raw_affiliation_strings":["18St. George's University Hospital, London, United Kingdom"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"18St. George's University Hospital, London, United Kingdom","institution_ids":["https://openalex.org/I165862685"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5026613738","display_name":"Emel \u00dcnal","orcid":"https://orcid.org/0000-0002-1966-2341","observed_orcids":["https://orcid.org/0000-0002-1966-2341"]},"institutions":[{"id":"https://openalex.org/I149218525","display_name":"Ankara University","ror":"https://ror.org/01wntqw50","country_code":"TR","type":"education","lineage":["https://openalex.org/I149218525"]}],"countries":["TR"],"is_corresponding":false,"raw_author_name":"Emel Unal","raw_affiliation_strings":["19Division of Pediatric Hematology/Oncology, Ankara University Faculty of Medicine, Department of Pediatrics - Division of Pediatric Hematology-Oncology, Ankara, Turkey., Istanbul, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"19Division of Pediatric Hematology/Oncology, Ankara University Faculty of Medicine, Department of Pediatrics - Division of Pediatric Hematology-Oncology, Ankara, Turkey., Istanbul, Turkey","institution_ids":["https://openalex.org/I149218525"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5113063285","display_name":"Depei Wu","orcid":"https://orcid.org/0000-0002-0050-9830","observed_orcids":["https://orcid.org/0000-0002-0050-9830"]},"institutions":[{"id":"https://openalex.org/I4210153519","display_name":"First Affiliated Hospital of Soochow University","ror":"https://ror.org/051jg5p78","country_code":"CN","type":"healthcare","lineage":["https://openalex.org/I4210153519"]}],"countries":["CN"],"is_corresponding":false,"raw_author_name":"Depei Wu","raw_affiliation_strings":["20National Clinical Research Center for Hematologic Diseases, Jiangsu Institute of Hematology, The First Affiliated Hospital of Soochow University, Institute of Blood and Marrow Transplantation of Soochow University, Suzhou, China"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"20National Clinical Research Center for Hematologic Diseases, Jiangsu Institute of Hematology, The First Affiliated Hospital of Soochow University, Institute of Blood and Marrow Transplantation of Soochow University, Suzhou, China","institution_ids":["https://openalex.org/I4210153519"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5036207495","display_name":"Patrice Chevallier","orcid":"https://orcid.org/0000-0003-3142-5581","observed_orcids":["https://orcid.org/0000-0003-3142-5581"]},"institutions":[{"id":"https://openalex.org/I3019204325","display_name":"Centre Hospitalier Universitaire de Nantes","ror":"https://ror.org/05c1qsg97","country_code":"FR","type":"healthcare","lineage":["https://openalex.org/I3019204325"]}],"countries":["FR"],"is_corresponding":false,"raw_author_name":"Patrice Chevallier","raw_affiliation_strings":["21Hematology Department, Nantes University Hospital, Nantes, France"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"21Hematology Department, Nantes University Hospital, Nantes, France","institution_ids":["https://openalex.org/I3019204325"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5089360800","display_name":"\u00c9douard Forcade","orcid":"https://orcid.org/0000-0002-8873-2868","observed_orcids":["https://orcid.org/0000-0002-8873-2868"]},"institutions":[{"id":"https://openalex.org/I3018323443","display_name":"Centre Hospitalier Universitaire de Bordeaux","ror":"https://ror.org/01hq89f96","country_code":"FR","type":"healthcare","lineage":["https://openalex.org/I3018323443"]}],"countries":["FR"],"is_corresponding":false,"raw_author_name":"Edouard Forcade","raw_affiliation_strings":["22Service d'H\u00e9matologie Clinique et Th\u00e9rapie Cellulaire, CHU Bordeaux, H\u00f4pital Haut-Leveque, Bordeaux, France"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"22Service d'H\u00e9matologie Clinique et Th\u00e9rapie Cellulaire, CHU Bordeaux, H\u00f4pital Haut-Leveque, Bordeaux, France","institution_ids":["https://openalex.org/I3018323443"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5025494836","display_name":"John Andrew Snowden","orcid":"https://orcid.org/0000-0001-6819-3476","observed_orcids":["https://orcid.org/0000-0001-6819-3476"]},"institutions":[{"id":"https://openalex.org/I91136226","display_name":"University of Sheffield","ror":"https://ror.org/05krs5044","country_code":"GB","type":"education","lineage":["https://openalex.org/I91136226"]}],"countries":["GB"],"is_corresponding":false,"raw_author_name":"John A. Snowden","raw_affiliation_strings":["23Sheffield University Teaching Hospitals, Sheffield, United Kingdom"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"23Sheffield University Teaching Hospitals, Sheffield, United Kingdom","institution_ids":["https://openalex.org/I91136226"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5014824633","display_name":"Hakan \u00d6zdo\u011fu","orcid":"https://orcid.org/0000-0002-8902-1283","observed_orcids":["https://orcid.org/0000-0002-8902-1283"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Hakan Ozdogu","raw_affiliation_strings":["24Hematology Division, BMT Unit, Haemaology Reserach Laboratory, Training & Medical, Baskent University Hospital, Adana, Turkey"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"24Hematology Division, BMT Unit, Haemaology Reserach Laboratory, Training & Medical, Baskent University Hospital, Adana, Turkey","institution_ids":[]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5049668306","display_name":"Antonio Maria Risitano","orcid":"https://orcid.org/0000-0002-4744-5109","observed_orcids":["https://orcid.org/0000-0002-4744-5109"]},"institutions":[{"id":"https://openalex.org/I4210111929","display_name":"Azienda Ospedaliera S.Giuseppe Moscati","ror":"https://ror.org/021jxzw96","country_code":"IT","type":"healthcare","lineage":["https://openalex.org/I4210111929"]}],"countries":["IT"],"is_corresponding":false,"raw_author_name":"Antonio Risitano","raw_affiliation_strings":["25Hematology and Hematopoietic Transplantation, AORN S. Giuseppe Moscati Avellino, Avellino, Italy"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"25Hematology and Hematopoietic Transplantation, AORN S. Giuseppe Moscati Avellino, Avellino, Italy","institution_ids":["https://openalex.org/I4210111929"]}]},{"author_position":"last","author":{"id":"https://openalex.org/A5080673678","display_name":"R\u00e9gis Peffault de Latour","orcid":"https://orcid.org/0000-0001-6222-4753","observed_orcids":["https://orcid.org/0000-0001-6222-4753"]},"institutions":[{"id":"https://openalex.org/I204730241","display_name":"Universit\u00e9 Paris Cit\u00e9","ror":"https://ror.org/05f82e368","country_code":"FR","type":"education","lineage":["https://openalex.org/I204730241"]},{"id":"https://openalex.org/I4210097159","display_name":"Assistance Publique \u2013 H\u00f4pitaux de Paris","ror":"https://ror.org/00pg5jh14","country_code":"FR","type":"healthcare","lineage":["https://openalex.org/I4210097159"]},{"id":"https://openalex.org/I4210144610","display_name":"H\u00f4pital Saint-Louis","ror":"https://ror.org/049am9t04","country_code":"FR","type":"healthcare","lineage":["https://openalex.org/I4210097159","https://openalex.org/I4210144610"]}],"countries":["FR"],"is_corresponding":false,"raw_author_name":"R\u00e9gis Peffault de Latour","raw_affiliation_strings":["26Assistance Publique-H\u00f4pitaux de Paris, Saint-Louis Hospital, Universit\u00e9 Paris Cit\u00e9, Paris, France","27French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Paris, France"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"26Assistance Publique-H\u00f4pitaux de Paris, Saint-Louis Hospital, Universit\u00e9 Paris Cit\u00e9, Paris, France","institution_ids":["https://openalex.org/I204730241","https://openalex.org/I4210097159","https://openalex.org/I4210144610"]},{"raw_affiliation_string":"27French Reference Center for Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria, Paris, France","institution_ids":[]}]}],"institutions":[],"countries_distinct_count":8,"institutions_distinct_count":32,"corresponding_author_ids":[],"corresponding_institution_ids":[],"apc_list":{"value":2500,"currency":"USD","value_usd":2500},"apc_paid":null,"fwci":0.0,"has_fulltext":false,"cited_by_count":0,"citation_normalized_percentile":{"value":0.15222395,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":null,"biblio":{"volume":"140","issue":"Supplement 1","first_page":"5799","last_page":"5800"},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T12919","display_name":"Blood disorders and treatments","score":0.8755000233650208,"subfield":{"id":"https://openalex.org/subfields/1311","display_name":"Genetics"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},"topics":[{"id":"https://openalex.org/T12919","display_name":"Blood disorders and treatments","score":0.8755000233650208,"subfield":{"id":"https://openalex.org/subfields/1311","display_name":"Genetics"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},{"id":"https://openalex.org/T10345","display_name":"Hematopoietic Stem Cell Transplantation","score":0.09200000017881393,"subfield":{"id":"https://openalex.org/subfields/2720","display_name":"Hematology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T13374","display_name":"Hematological disorders and diagnostics","score":0.013799999840557575,"subfield":{"id":"https://openalex.org/subfields/2711","display_name":"Emergency Medicine"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/androgens","display_name":"androgens","score":0.9419999718666077},{"id":"https://openalex.org/keywords/severe-aplastic-anemia","display_name":"severe aplastic anemia","score":0.9110000133514404},{"id":"https://openalex.org/keywords/dyskeratosis-congenita","display_name":"dyskeratosis congenita","score":0.8389999866485596},{"id":"https://openalex.org/keywords/fanconi-anemia","display_name":"Fanconi anemia","score":1.0},{"id":"https://openalex.org/keywords/oxymetholone","display_name":"oxymetholone","score":0.8379999995231628},{"id":"https://openalex.org/keywords/prednisolone","display_name":"prednisolone","score":0.5529999732971191},{"id":"https://openalex.org/keywords/antithymocyte-globulin","display_name":"antithymocyte globulin","score":0.746999979019165},{"id":"https://openalex.org/keywords/treatment-outcomes","display_name":"treatment outcomes","score":0.5090000033378601},{"id":"https://openalex.org/keywords/transfusion-dependence","display_name":"transfusion dependence","score":0.578000009059906},{"id":"https://openalex.org/keywords/relapse","display_name":"relapse","score":0.33000001311302185},{"id":"https://openalex.org/keywords/long-term-effects","display_name":"long-term effects","score":0.38999998569488525},{"id":"https://openalex.org/keywords/real-world-treatment-patterns","display_name":"real-world treatment patterns","score":0.5339999794960022}],"concepts":[{"id":"https://openalex.org/C71924100","wikidata":"https://www.wikidata.org/wiki/Q11190","display_name":"Medicine","level":0,"score":0.7047790288925171},{"id":"https://openalex.org/C2779285011","wikidata":"https://www.wikidata.org/wiki/Q3709312","display_name":"Dyskeratosis congenita","level":4,"score":0.6648395657539368},{"id":"https://openalex.org/C2780525284","wikidata":"https://www.wikidata.org/wiki/Q7882181","display_name":"Bone marrow failure","level":4,"score":0.6023158431053162},{"id":"https://openalex.org/C2781440808","wikidata":"https://www.wikidata.org/wiki/Q846316","display_name":"Aplastic anemia","level":3,"score":0.5717329382896423},{"id":"https://openalex.org/C2911091166","wikidata":"https://www.wikidata.org/wiki/Q106419912","display_name":"Transplantation","level":2,"score":0.495169073343277},{"id":"https://openalex.org/C126322002","wikidata":"https://www.wikidata.org/wiki/Q11180","display_name":"Internal medicine","level":1,"score":0.42880934476852417},{"id":"https://openalex.org/C2780007613","wikidata":"https://www.wikidata.org/wiki/Q546523","display_name":"Bone marrow","level":2,"score":0.41342952847480774},{"id":"https://openalex.org/C143998085","wikidata":"https://www.wikidata.org/wiki/Q162555","display_name":"Oncology","level":1,"score":0.34599512815475464},{"id":"https://openalex.org/C187212893","wikidata":"https://www.wikidata.org/wiki/Q123028","display_name":"Pediatrics","level":1,"score":0.3349437117576599},{"id":"https://openalex.org/C28328180","wikidata":"https://www.wikidata.org/wiki/Q48196","display_name":"Stem cell","level":2,"score":0.22866377234458923},{"id":"https://openalex.org/C109159458","wikidata":"https://www.wikidata.org/wiki/Q919283","display_name":"Haematopoiesis","level":3,"score":0.15174967050552368},{"id":"https://openalex.org/C86803240","wikidata":"https://www.wikidata.org/wiki/Q420","display_name":"Biology","level":0,"score":0.11758440732955933},{"id":"https://openalex.org/C552990157","wikidata":"https://www.wikidata.org/wiki/Q7430","display_name":"DNA","level":2,"score":0.0},{"id":"https://openalex.org/C54355233","wikidata":"https://www.wikidata.org/wiki/Q7162","display_name":"Genetics","level":1,"score":0.0},{"id":"https://openalex.org/C177336024","wikidata":"https://www.wikidata.org/wiki/Q14872779","display_name":"Telomere","level":3,"score":0.0}],"mesh":[],"locations_count":1,"locations":[{"id":"doi:10.1182/blood-2022-169086","doi":"https://doi.org/10.1182/blood-2022-169086","is_oa":false,"landing_page_url":"https://doi.org/10.1182/blood-2022-169086","pdf_url":null,"source":{"id":"https://openalex.org/S200071133","display_name":"Blood","issn_l":"0006-4971","issn":["0006-4971","1528-0020"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-a","doyens","jufo-3","ki-jl-3","medline","norway-2","poland-200","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Blood","raw_type":"journal-article"}],"best_oa_location":null,"sustainable_development_goals":[{"id":"https://metadata.un.org/sdg/3","score":1.0,"display_name":"Good health and well-being"}],"study_designs":[{"id":"https://openalex.org/study-designs/observational-study","display_name":"Observational Study"}],"awards":[],"funders":[],"has_content":{"pdf":false,"grobid_xml":false},"content_urls":null,"referenced_works_count":0,"referenced_works":[],"related_works":["https://openalex.org/W4377011771","https://openalex.org/W4385850755","https://openalex.org/W4377939147","https://openalex.org/W4386573990","https://openalex.org/W2779449343","https://openalex.org/W2251058624","https://openalex.org/W3010413675","https://openalex.org/W2979342251","https://openalex.org/W2433783511","https://openalex.org/W70268494"],"abstract_inverted_index":{"Anabolic":[0],"steroids":[1],"have":[2,56,97],"been":[3,57,99],"used":[4,58,300],"for":[5,89,117,219,224,421,425,430,454,460,486],"several":[6],"decades":[7],"in":[8,69,74,82,102,124,137,167,175,180,186,281,363,369,573,614,654],"inherited":[9,30,122,179,225,256,370,455,657],"and":[10,25,36,67,95,134,139,154,178,192,221,239,284,312,355,361,365,367,427,456,474,508,523,528,540,561,566,575,622,628,641,648,656],"acquired":[11,53,174,220,260,364,461],"bone":[12],"marrow":[13],"failure":[14,433],"(BMF),":[15],"due":[16],"to":[17,60,71,126,232,291,414,445,493,499,650],"their":[18,91,128],"pleiotropic":[19],"effects":[20,136,530,569],"on":[21,145],"erythrogenesis,":[22],"telomere":[23],"regulation":[24],"immune":[26],"homeostasis.":[27],"In":[28,52,244,267,325,374,599],"some":[29],"disorders,":[31],"mainly":[32],"Dyskeratosis":[33],"Congenita":[34],"(DC)":[35],"Fanconi":[37],"anemia":[38],"(FA),":[39],"they":[40,55],"still":[41,81,613],"represent":[42],"one":[43],"of":[44,63,85,113,169,212,255,259,286,294,318,327,378,393,407,437,481,520,538,551,577,591,620,625,633],"the":[45,61,83,108,170,210,268,287,292,328,390,547,578,610],"main":[46],"non-transplant":[47],"approaches,":[48],"achieving":[49],"satisfactory":[50],"outcomes.":[51],"setting,":[54],"prior":[59],"availability":[62],"anti-thymocyte":[64],"globulin":[65],"(ATG)":[66],"subsequently,":[68],"combination":[70],"it,":[72],"or":[73,120,278,412],"refractory/relapsed":[75],"patients":[76,114,147,248,372,377,602],"with":[77,162,501,616,637],"heterogeneous":[78],"results.":[79],"Albeit":[80],"armamentarium":[84],"possible":[86],"therapeutic":[87],"options":[88],"BMF,":[90,123,226],"place,":[92],"optimal":[93],"timing,":[94],"dosage":[96],"never":[98],"formally":[100],"defined":[101],"aplastic":[103],"disorders.":[104],"Here":[105],"we":[106,489],"assembled":[107],"so":[109],"far":[110],"largest":[111],"cohort":[112,380],"receiving":[115,148],"androgens":[116,263],"an":[118,121,149,383],"idiopathic":[119,269,655],"order":[125],"track":[127],"current":[129],"real-life":[130],"use,":[131],"indications,":[132],"outcomes,":[133],"long-term":[135,482],"European":[138],"EBMT-affiliated":[140],"centers.":[141,158],"We":[142],"collected":[143],"data":[144,484],"274":[146],"androgen":[150,213,234,319,352,399,441,467],"treatment":[151,252,320,515],"between":[152],"1990":[153],"2021":[155],"across":[156],"82":[157],"Patients":[159],"were":[160,249,273,359,490,511,531,570,586],"diagnosed":[161],"a":[163,330,518,536,604,617],"severe/very":[164],"severe":[165],"BMF":[166,371],"74%":[168],"cases.":[171],"Etiology":[172],"was":[173,205,215,236,297,321,336,340,417,450,469,546],"71%":[176],"(N=192)":[177],"29%":[181],"(N=78,":[182],"missing":[183],"N=4),":[184],"with,":[185],"this":[187,379,631],"last":[188],"group,":[189],"FA":[190],"(88%)":[191],"DC":[193],"(11%)":[194],"being":[195,438],"predominant,":[196],"followed":[197,302,557],"by":[198,303,558],"fewer":[199],"other":[200,265,597],"indications":[201],"(1%).":[202],"Male/Female":[203],"ratio":[204],"1.5.":[206],"Median":[207,338],"age":[208],"at":[209,389,555,581,593,606],"time":[211,229,392,608],"start":[214],"32":[216],"(18-52)":[217],"years":[218,595],"8":[222],"(6-12)":[223],"while":[227,505],"median":[228,316,391,519,537],"from":[230,398],"diagnosis":[231],"first":[233],"use":[235,615,643],"4":[237],"(0.3-17.6)":[238],"8.5":[240],"(0.4-34.9)":[241],"months":[242,323,342,350,395,525,542],"respectively.":[243,289,373,478],"most":[245,298,548],"cases":[246,261,329,579,652],"(78%),":[247],"transfusion-dependent":[250],"upon":[251],"initiation;":[253],"91%":[254],"versus":[257],"54%":[258],"received":[262,382],"before":[264,596],"therapies.":[266],"setting":[270],"these":[271],"compounds":[272],"administered":[274],"as":[275],"2nd":[276],",3rd":[277],"further":[279,446],"line":[280],"23%,":[282],"13%":[283,360,451],"10%":[285],"patients,":[288,488],"As":[290],"type":[293,550],"molecules,":[295],"oxymetholone":[296],"commonly":[299],"(48%),":[301],"danazol":[304],"(32%),":[305],"norethandrolone":[306],"(11%),":[307],"nandrolone":[308],"(2%),":[309],"testosterone":[310],"(4%)":[311],"others":[313],"(3%).":[314],"Overall,":[315],"duration":[317],"9":[322],"(IQR:3-26).":[324],"60%":[326],"concomitant":[331],"immunosuppressive":[332],"therapy":[333],"(mainly":[334],"cyclosporine)":[335],"administered.":[337],"follow-up":[339,483],"77.6":[341],"(95%":[343],"CI":[344],"65.3":[345],"-":[346],"96).":[347],"At":[348],"six":[349],"after":[351,440,466,514,535],"treatment,":[353,442],"complete":[354],"partial":[356],"response":[357,639],"rates":[358,640],"37%":[362],"4.5%":[366],"40.9%":[368],"total,":[375],"160":[376],"(58%)":[381],"allogeneic":[384],"hematopoietic":[385],"cell":[386],"transplantation":[387],"(HCT)":[388],"18.4":[394],"(IQR:":[396],"7-43.9)":[397],"initiation.":[400],"The":[401],"5-year":[402],"post-androgen":[403],"cumulative":[404],"incidence":[405],"(CI)":[406],"clonal":[408,626],"events":[409,627],"(leukemic":[410],"transformation":[411],"evolution":[413],"secondary":[415,629],"PNH)":[416],"1%":[418,428,574,592],"(95%CI":[419,452,458,472,476],"0-2%)":[420],"PNH,":[422],"3%":[423],"(1-6%)":[424],"MDS":[426],"(0%-3%)":[429],"AML.":[431],"Five-year":[432,463],"free":[434],"survival":[435,465],"(probability":[436],"alive":[439],"without":[443],"switching":[444],"lines,":[447],"including":[448],"HCT),":[449],"6-21%)":[453],"23%":[457],"16-30%)":[459],"BMF.":[462],"overall":[464],"initiation":[468,516],"instead":[470],"79%":[471],"69-88%)":[473],"64%":[475],"56-71%)":[477],"Taking":[479],"advantage":[480],"available":[485],"89":[487],"also":[491,587],"able":[492],"highlight":[494],"androgen-related":[495],"toxicities":[496,510,563],"that":[497],"tended":[498],"occur":[500],"variable":[502],"post-treatment":[503],"intervals:":[504],"liver,":[506],"renal":[507,562],"gastro-intestinal":[509,559],"encountered":[512],"early":[513],"(at":[517],"3.4,":[521],"5.4":[522],"6.4":[524],"respectively),":[526],"endocrinological":[527],"psychiatric":[529],"more":[532],"delayed":[533],"(occurring":[534],"15.1":[539],"18.1":[541],"respectively).":[543],"Liver":[544],"dysfunction":[545],"frequent":[549],"side":[552,568],"effect":[553],"(10%)":[554],"1-year,":[556],"(3%)":[560],"(2%).":[564],"Psychiatric":[565],"endocrine":[567],"rare,":[571],"reported":[572],"2%":[576],"respectively":[580],"3":[582,594,601],"years.":[583],"Solid":[584],"neoplasms":[585],"rarely":[588],"observed":[589],"(CI":[590],"treatments).":[598],"total":[600],"developed":[603],"neoplasia":[605],"any":[607],"during":[609],"follow-up.":[611],"While":[612],"manageable":[618],"level":[619],"toxicities,":[621],"low":[623,638],"rate":[624],"neoplasia,":[630],"category":[632],"therapeutics":[634],"remains":[635],"associated":[636],"its":[642],"should":[644],"be":[645],"carefully":[646],"evaluated":[647],"reserved":[649],"selected":[651],"both":[653],"setting.":[658]},"counts_by_year":[],"updated_date":"2026-10-26T11:51:55.731654","created_date":"2022-11-30T00:00:00"}
