{"id":"https://openalex.org/W4283816259","doi":"https://doi.org/10.1016/s0168-8278(22)01365-4","title":"Efficacy and safety of odevixibat over 72 weeks of treatment in patients with progressive familial intrahepatic cholestasis","display_name":"Efficacy and safety of odevixibat over 72 weeks of treatment in patients with progressive familial intrahepatic cholestasis","publication_year":2022,"publication_date":"2022-07-01","ids":{"openalex":"https://openalex.org/W4283816259","doi":"https://doi.org/10.1016/s0168-8278(22)01365-4"},"language":"en","primary_location":{"id":"doi:10.1016/s0168-8278(22)01365-4","doi":"https://doi.org/10.1016/s0168-8278(22)01365-4","is_oa":false,"landing_page_url":"https://doi.org/10.1016/s0168-8278(22)01365-4","pdf_url":null,"source":{"id":"https://openalex.org/S83651209","display_name":"Journal of Hepatology","issn_l":"0168-8278","issn":["0168-8278","1600-0641"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-a","doyens","jufo-3","ki-jl-3","medline","norway-2","poland-200","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Journal of Hepatology","raw_type":"journal-article"},"volume":null,"type":"article","indexed_in":["crossref"],"open_access":{"is_oa":false,"oa_status":"closed","oa_url":null,"any_repository_has_fulltext":false},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5002550781","display_name":"Richard J. Thompson","orcid":"https://orcid.org/0000-0001-5652-0150","observed_orcids":["https://orcid.org/0000-0001-5652-0150"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Richard J. Thompson","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5011058995","display_name":"Emmanuel M. Gonzales","orcid":"https://orcid.org/0000-0002-1546-3193","observed_orcids":["https://orcid.org/0000-0002-1546-3193"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Emmanuel Gonzal\u00e8s","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5000280651","display_name":"Reha Artan","orcid":"https://orcid.org/0000-0001-6114-9210","observed_orcids":["https://orcid.org/0000-0001-6114-9210"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Reha Artan","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5037877031","display_name":"Winita Hardikar","orcid":"https://orcid.org/0000-0003-4277-2773","observed_orcids":["https://orcid.org/0000-0003-4277-2773"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Winita Hardikar","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5072966366","display_name":"Florence Lacaille","orcid":"https://orcid.org/0000-0002-5272-4970","observed_orcids":["https://orcid.org/0000-0002-5272-4970"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Florence Lacaille","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5081268394","display_name":"Alain Lachaux","orcid":"https://orcid.org/0000-0003-3852-788X","observed_orcids":["https://orcid.org/0000-0003-3852-788X"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Alain Lachaux","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5082630677","display_name":"Bertrand Roquelaure","orcid":"https://orcid.org/0009-0003-3366-2334","observed_orcids":["https://orcid.org/0009-0003-3366-2334"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Bertrand Roquelaure","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5012844484","display_name":"Ulrich Baumann","orcid":"https://orcid.org/0000-0002-0162-0266","observed_orcids":["https://orcid.org/0000-0002-0162-0266"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Ulrich Baumann","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5066163290","display_name":"Ekkehard Sturm","orcid":"https://orcid.org/0000-0002-1489-8662","observed_orcids":["https://orcid.org/0000-0002-1489-8662"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Ekkehard Sturm","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5086781425","display_name":"Eyal Shteyer","orcid":"https://orcid.org/0000-0002-8288-1272","observed_orcids":["https://orcid.org/0000-0002-8288-1272"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Eyal Shteyer","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5055569132","display_name":"Pier Luigi Calvo","orcid":"https://orcid.org/0000-0001-9264-3465","observed_orcids":["https://orcid.org/0000-0001-9264-3465"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Pier Luigi Calvo","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5031718124","display_name":"Henkjan J. Verkade","orcid":"https://orcid.org/0000-0002-7034-2861","observed_orcids":["https://orcid.org/0000-0002-7034-2861"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Henkjan J. Verkade","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5045989725","display_name":"Mohammad Ali Shagrani","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Mohammad Ali Shagrani","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5111529500","display_name":"Janis M. Stoll","orcid":"https://orcid.org/0000-0001-9689-4675","observed_orcids":["https://orcid.org/0000-0001-9689-4675"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Janis M. Stoll","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5065353690","display_name":"Piotr Czubkowski","orcid":"https://orcid.org/0000-0002-0332-5703","observed_orcids":["https://orcid.org/0000-0002-0332-5703"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Piotr Czubkowski","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5081370839","display_name":"Buket Dalg\u0131\u00e7","orcid":"https://orcid.org/0000-0003-4678-8764","observed_orcids":["https://orcid.org/0000-0003-4678-8764"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Buket Dalg\u0131\u00e7","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5036764010","display_name":"Girish L. Gupte","orcid":"https://orcid.org/0000-0002-9026-1583","observed_orcids":["https://orcid.org/0000-0002-9026-1583"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Girish Gupte","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5019267788","display_name":"Tassos Grammatikopoulos","orcid":"https://orcid.org/0000-0002-0174-4787","observed_orcids":["https://orcid.org/0000-0002-0174-4787"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Tassos Grammatikopoulos","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5069377290","display_name":"Patrick James McKiernan","orcid":"https://orcid.org/0000-0002-8466-8504","observed_orcids":["https://orcid.org/0000-0002-8466-8504"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Patrick McKiernan","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":null,"display_name":"Qifeng Yu","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Qifeng Yu","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5068834676","display_name":"Lise Kjems","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Lise Kjems","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"last","author":{"id":null,"display_name":"Patrick Horn","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Patrick Horn","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]}],"institutions":[],"countries_distinct_count":0,"institutions_distinct_count":0,"corresponding_author_ids":[],"corresponding_institution_ids":[],"apc_list":{"value":4500,"currency":"USD","value_usd":4500},"apc_paid":null,"fwci":0.24,"has_fulltext":false,"cited_by_count":1,"citation_normalized_percentile":{"value":0.49373905,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":{"min":90,"max":94},"biblio":{"volume":"77","issue":null,"first_page":"S521","last_page":"S521"},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T12460","display_name":"Pediatric Hepatobiliary Diseases and Treatments","score":0.5737000107765198,"subfield":{"id":"https://openalex.org/subfields/2746","display_name":"Surgery"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},"topics":[{"id":"https://openalex.org/T12460","display_name":"Pediatric Hepatobiliary Diseases and Treatments","score":0.5737000107765198,"subfield":{"id":"https://openalex.org/subfields/2746","display_name":"Surgery"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T10570","display_name":"Drug Transport and Resistance Mechanisms","score":0.365200012922287,"subfield":{"id":"https://openalex.org/subfields/2730","display_name":"Oncology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T11834","display_name":"Liver Diseases and Immunity","score":0.008700000122189522,"subfield":{"id":"https://openalex.org/subfields/2721","display_name":"Hepatology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/odevixibat","display_name":"odevixibat","score":1.0},{"id":"https://openalex.org/keywords/progressive-familial-intrahepatic-cholestasis","display_name":"progressive familial intrahepatic cholestasis","score":0.9929999709129333},{"id":"https://openalex.org/keywords/cholestatic-liver-disease","display_name":"cholestatic liver disease","score":0.7710000276565552},{"id":"https://openalex.org/keywords/long-term-efficacy","display_name":"long-term efficacy","score":0.6840000152587891},{"id":"https://openalex.org/keywords/drug-safety","display_name":"drug safety","score":0.8370000123977661}],"concepts":[{"id":"https://openalex.org/C2778593092","wikidata":"https://www.wikidata.org/wiki/Q1075923","display_name":"Cholestasis","level":2,"score":0.8385545611381531},{"id":"https://openalex.org/C2778132995","wikidata":"https://www.wikidata.org/wiki/Q1018534","display_name":"Progressive familial intrahepatic cholestasis","level":4,"score":0.8355525135993958},{"id":"https://openalex.org/C71924100","wikidata":"https://www.wikidata.org/wiki/Q11190","display_name":"Medicine","level":0,"score":0.706109881401062},{"id":"https://openalex.org/C90924648","wikidata":"https://www.wikidata.org/wiki/Q120569","display_name":"Gastroenterology","level":1,"score":0.47925400733947754},{"id":"https://openalex.org/C126322002","wikidata":"https://www.wikidata.org/wiki/Q11180","display_name":"Internal medicine","level":1,"score":0.45592382550239563},{"id":"https://openalex.org/C187212893","wikidata":"https://www.wikidata.org/wiki/Q123028","display_name":"Pediatrics","level":1,"score":0.3696061372756958},{"id":"https://openalex.org/C2779609443","wikidata":"https://www.wikidata.org/wiki/Q1368191","display_name":"Liver transplantation","level":3,"score":0.03945162892341614},{"id":"https://openalex.org/C2911091166","wikidata":"https://www.wikidata.org/wiki/Q106419912","display_name":"Transplantation","level":2,"score":0.0}],"mesh":[],"locations_count":3,"locations":[{"id":"doi:10.1016/s0168-8278(22)01365-4","doi":"https://doi.org/10.1016/s0168-8278(22)01365-4","is_oa":false,"landing_page_url":"https://doi.org/10.1016/s0168-8278(22)01365-4","pdf_url":null,"source":{"id":"https://openalex.org/S83651209","display_name":"Journal of Hepatology","issn_l":"0168-8278","issn":["0168-8278","1600-0641"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-a","doyens","jufo-3","ki-jl-3","medline","norway-2","poland-200","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Journal of Hepatology","raw_type":"journal-article"},{"id":"pmh:oai:pure.rug.nl:openaire_cris_publications/89aab6fe-7f82-4226-8ce6-f243e861ce1e","doi":null,"is_oa":false,"landing_page_url":"https://hdl.handle.net/11370/89aab6fe-7f82-4226-8ce6-f243e861ce1e","pdf_url":null,"source":{"id":"https://openalex.org/S4306400420","display_name":"University of Groningen research database (University of Groningen / Centre for Information Technology)","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/I169381384","host_organization_name":"University of Groningen","host_organization_lineage":["https://openalex.org/I169381384"],"host_organization_lineage_names":[],"type":"repository"},"license":null,"license_id":null,"version":"submittedVersion","is_accepted":false,"is_published":false,"raw_source_name":"Thompson, R J, Gonzales, E, Artan, R, Hardikar, W, Lacaille, F, Lachaux, A, Roquelaure, B, Baumann, U, Sturm, E, Shteyer, E, Calvo, P L, Verkade, H J, Shagrani, M A, Stoll, J M, Czubkowski, P, Dalgic, B, Gupte, G, Grammatikopoulos, T, McKiernan, P, Yu, Q, Kjems, L & Horn, P 2022, 'Efficacy and safety of odevixibat over 72 weeks of treatment in patients with progressive familial intrahepatic cholestasis', Journal of Hepatology, vol. 77, pp. S521-S521.","raw_type":"info:eu-repo/semantics/conferenceObject"},{"id":"pmh:rug:oai:pure.rug.nl:publications/89aab6fe-7f82-4226-8ce6-f243e861ce1e","doi":null,"is_oa":false,"landing_page_url":"https://research.rug.nl/en/publications/89aab6fe-7f82-4226-8ce6-f243e861ce1e","pdf_url":null,"source":{"id":"https://openalex.org/S4306400420","display_name":"University of Groningen research database (University of Groningen / Centre for Information Technology)","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/I169381384","host_organization_name":"University of Groningen","host_organization_lineage":["https://openalex.org/I169381384"],"host_organization_lineage_names":[],"type":"repository"},"license":null,"license_id":null,"version":"submittedVersion","is_accepted":false,"is_published":false,"raw_source_name":"Journal of Hepatology, 77, S521 - S521. ELSEVIER SCIENCE BV","raw_type":"info:eu-repo/semantics/article"}],"best_oa_location":null,"sustainable_development_goals":[{"display_name":"Good health and well-being","id":"https://metadata.un.org/sdg/3","score":1.0}],"study_designs":[],"awards":[],"funders":[],"has_content":{"grobid_xml":false,"pdf":false},"content_urls":null,"referenced_works_count":0,"referenced_works":[],"related_works":["https://openalex.org/W4384946690","https://openalex.org/W4410138533","https://openalex.org/W4399536764","https://openalex.org/W4384942732","https://openalex.org/W4287306769","https://openalex.org/W7140142008","https://openalex.org/W4384942310","https://openalex.org/W4283808836","https://openalex.org/W7065625268","https://openalex.org/W4385307042"],"abstract_inverted_index":null,"counts_by_year":[{"year":2025,"cited_by_count":1}],"updated_date":"2026-10-19T09:35:57.686232","created_date":"2022-07-06T00:00:00"}
