{"id":"https://openalex.org/W3147515775","doi":"https://doi.org/10.1016/j.nmd.2020.08.211","title":"DMD \u2013 ANIMAL MODELS & PRECLINICAL TREATMENT","display_name":"DMD \u2013 ANIMAL MODELS & PRECLINICAL TREATMENT","publication_year":2020,"publication_date":"2020-09-28","ids":{"openalex":"https://openalex.org/W3147515775","doi":"https://doi.org/10.1016/j.nmd.2020.08.211","mag":"3147515775"},"language":"en","primary_location":{"id":"doi:10.1016/j.nmd.2020.08.211","doi":"https://doi.org/10.1016/j.nmd.2020.08.211","is_oa":false,"landing_page_url":"https://doi.org/10.1016/j.nmd.2020.08.211","pdf_url":null,"source":{"id":"https://openalex.org/S50004817","display_name":"Neuromuscular Disorders","issn_l":"0960-8966","issn":["0960-8966","1873-2364"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["cwts-core","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","poland-100","russia-white-list-2","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Neuromuscular Disorders","raw_type":"journal-article"},"volume":null,"type":"article","indexed_in":["crossref"],"open_access":{"is_oa":false,"oa_status":"closed","oa_url":null,"any_repository_has_fulltext":false},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5102720102","display_name":"Alan John Russell","orcid":"https://orcid.org/0000-0001-7545-5008","observed_orcids":["https://orcid.org/0000-0001-7545-5008"]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"A. Russell","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]},{"author_position":"middle","author":{"id":null,"display_name":"M. DuVall","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"M. DuVall","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5003632714","display_name":"Breanne L. Newell\u2010Stamper","orcid":"https://orcid.org/0000-0002-5098-1965","observed_orcids":["https://orcid.org/0000-0002-5098-1965"]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"B. Stamper","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5113625275","display_name":"B. Robertson","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"B. Robertson","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]},{"author_position":"middle","author":{"id":null,"display_name":"S. Schlachter","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"S. Schlachter","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]},{"author_position":"middle","author":{"id":null,"display_name":"K. Hunt","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"K. Hunt","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5030724519","display_name":"Yeqing Qian","orcid":"https://orcid.org/0000-0002-5570-8423","observed_orcids":["https://orcid.org/0000-0002-5570-8423"]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Y. Qian","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]},{"author_position":"middle","author":{"id":null,"display_name":"A. Powers","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"A. Powers","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5050836346","display_name":"Dennis R. Claflin","orcid":"https://orcid.org/0000-0001-8044-0142","observed_orcids":["https://orcid.org/0000-0001-8044-0142"]},"institutions":[{"id":"https://openalex.org/I27837315","display_name":"University of Michigan","ror":"https://ror.org/00jmfr291","country_code":"US","type":"education","lineage":["https://openalex.org/I27837315"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"D. Claflin","raw_affiliation_strings":["University of Michigan, Ann Arbor, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"University of Michigan, Ann Arbor, USA","institution_ids":["https://openalex.org/I27837315"]}]},{"author_position":"middle","author":{"id":null,"display_name":"Y. Su","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I27837315","display_name":"University of Michigan","ror":"https://ror.org/00jmfr291","country_code":"US","type":"education","lineage":["https://openalex.org/I27837315"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"Y. Su","raw_affiliation_strings":["University of Michigan, Ann Arbor, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"University of Michigan, Ann Arbor, USA","institution_ids":["https://openalex.org/I27837315"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5002008484","display_name":"Susan V. Brooks","orcid":"https://orcid.org/0000-0003-1954-967X","observed_orcids":["https://orcid.org/0000-0003-1954-967X"]},"institutions":[{"id":"https://openalex.org/I27837315","display_name":"University of Michigan","ror":"https://ror.org/00jmfr291","country_code":"US","type":"education","lineage":["https://openalex.org/I27837315"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"S. Brooks","raw_affiliation_strings":["University of Michigan, Ann Arbor, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"University of Michigan, Ann Arbor, USA","institution_ids":["https://openalex.org/I27837315"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5024097905","display_name":"Alexis M. Rutledge","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I91045830","display_name":"Texas A&M University","ror":"https://ror.org/01f5ytq51","country_code":"US","type":"education","lineage":["https://openalex.org/I91045830"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"A. Rutledge","raw_affiliation_strings":["Texas A&M University, College Station, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Texas A&M University, College Station, USA","institution_ids":["https://openalex.org/I91045830"]}]},{"author_position":"middle","author":{"id":"https://openalex.org/A5071737472","display_name":"Peter P. Nghiem","orcid":"https://orcid.org/0000-0002-8796-8123","observed_orcids":["https://orcid.org/0000-0002-8796-8123"]},"institutions":[{"id":"https://openalex.org/I91045830","display_name":"Texas A&M University","ror":"https://ror.org/01f5ytq51","country_code":"US","type":"education","lineage":["https://openalex.org/I91045830"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"P. Nghiem","raw_affiliation_strings":["Texas A&M University, College Station, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Texas A&M University, College Station, USA","institution_ids":["https://openalex.org/I91045830"]}]},{"author_position":"last","author":{"id":null,"display_name":"K. Koch","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I4387153259","display_name":"Edgewise Therapeutics (United States)","ror":"https://ror.org/03phcd550","country_code":"US","type":"company","lineage":["https://openalex.org/I4387153259"]}],"countries":["US"],"is_corresponding":false,"raw_author_name":"K. Koch","raw_affiliation_strings":["Edgewise Therapeutics, Boulder, USA"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"Edgewise Therapeutics, Boulder, USA","institution_ids":["https://openalex.org/I4387153259"]}]}],"institutions":[],"countries_distinct_count":1,"institutions_distinct_count":3,"corresponding_author_ids":[],"corresponding_institution_ids":[],"apc_list":{"value":3200,"currency":"USD","value_usd":3200},"apc_paid":null,"fwci":0.0811,"has_fulltext":false,"cited_by_count":1,"citation_normalized_percentile":{"value":0.37528583,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":{"min":89,"max":93},"biblio":{"volume":"30","issue":null,"first_page":"S108","last_page":"S108"},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T10441","display_name":"Muscle Physiology and Disorders","score":0.9994999766349792,"subfield":{"id":"https://openalex.org/subfields/1312","display_name":"Molecular Biology"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},"topics":[{"id":"https://openalex.org/T10441","display_name":"Muscle Physiology and Disorders","score":0.9994999766349792,"subfield":{"id":"https://openalex.org/subfields/1312","display_name":"Molecular Biology"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},{"id":"https://openalex.org/T12400","display_name":"Neurogenetic and Muscular Disorders Research","score":0.0003000000142492354,"subfield":{"id":"https://openalex.org/subfields/2716","display_name":"Genetics"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T10882","display_name":"Cardiomyopathy and Myosin Studies","score":9.999999747378752e-05,"subfield":{"id":"https://openalex.org/subfields/2705","display_name":"Cardiology and Cardiovascular Medicine"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/duchenne-muscular-dystrophy","display_name":"Duchenne muscular dystrophy","score":0.9909999966621399},{"id":"https://openalex.org/keywords/mdx-mice","display_name":"mdx mice","score":0.7519999742507935},{"id":"https://openalex.org/keywords/golden-retriever-muscular-dystrophy","display_name":"golden retriever muscular dystrophy","score":0.8169999718666077},{"id":"https://openalex.org/keywords/becker-muscular-dystrophy","display_name":"Becker muscular dystrophy","score":0.9599999785423279},{"id":"https://openalex.org/keywords/limb-girdle-muscular-dystrophy","display_name":"limb-girdle muscular dystrophy","score":0.925000011920929},{"id":"https://openalex.org/keywords/creatine-kinase","display_name":"creatine kinase","score":0.753000020980835},{"id":"https://openalex.org/keywords/muscle-fibrosis","display_name":"muscle fibrosis","score":0.7990000247955322},{"id":"https://openalex.org/keywords/exercise-induced-muscle-damage","display_name":"exercise-induced muscle damage","score":0.8240000009536743},{"id":"https://openalex.org/keywords/calcium-influx","display_name":"calcium influx","score":0.5669999718666077},{"id":"https://openalex.org/keywords/myofiber-degeneration","display_name":"myofiber degeneration","score":0.7390000224113464},{"id":"https://openalex.org/keywords/small-molecule-therapy","display_name":"small molecule therapy","score":0.5339999794960022}],"concepts":[{"id":"https://openalex.org/C2778943923","wikidata":"https://www.wikidata.org/wiki/Q1648484","display_name":"Duchenne muscular dystrophy","level":2,"score":0.7711132764816284},{"id":"https://openalex.org/C2779959927","wikidata":"https://www.wikidata.org/wiki/Q1048687","display_name":"Skeletal muscle","level":2,"score":0.6039087772369385},{"id":"https://openalex.org/C2779030066","wikidata":"https://www.wikidata.org/wiki/Q1137767","display_name":"Muscular dystrophy","level":2,"score":0.5506887435913086},{"id":"https://openalex.org/C36880943","wikidata":"https://www.wikidata.org/wiki/Q409458","display_name":"Creatine kinase","level":2,"score":0.5184142589569092},{"id":"https://openalex.org/C2779343474","wikidata":"https://www.wikidata.org/wiki/Q3109175","display_name":"Context (archaeology)","level":2,"score":0.5039014220237732},{"id":"https://openalex.org/C126322002","wikidata":"https://www.wikidata.org/wiki/Q11180","display_name":"Internal medicine","level":1,"score":0.48215338587760925},{"id":"https://openalex.org/C207200792","wikidata":"https://www.wikidata.org/wiki/Q428914","display_name":"Myocyte","level":2,"score":0.4358358681201935},{"id":"https://openalex.org/C134018914","wikidata":"https://www.wikidata.org/wiki/Q162606","display_name":"Endocrinology","level":1,"score":0.4316234886646271},{"id":"https://openalex.org/C2778750056","wikidata":"https://www.wikidata.org/wiki/Q24976962","display_name":"mdx mouse","level":4,"score":0.4305976331233978},{"id":"https://openalex.org/C163415756","wikidata":"https://www.wikidata.org/wiki/Q126473","display_name":"Contraction (grammar)","level":2,"score":0.42601025104522705},{"id":"https://openalex.org/C71924100","wikidata":"https://www.wikidata.org/wiki/Q11190","display_name":"Medicine","level":0,"score":0.4191814064979553},{"id":"https://openalex.org/C2780394045","wikidata":"https://www.wikidata.org/wiki/Q412285","display_name":"Dystrophin","level":3,"score":0.261044979095459},{"id":"https://openalex.org/C86803240","wikidata":"https://www.wikidata.org/wiki/Q420","display_name":"Biology","level":0,"score":0.1538456380367279},{"id":"https://openalex.org/C151730666","wikidata":"https://www.wikidata.org/wiki/Q7205","display_name":"Paleontology","level":1,"score":0.0}],"mesh":[],"locations_count":1,"locations":[{"id":"doi:10.1016/j.nmd.2020.08.211","doi":"https://doi.org/10.1016/j.nmd.2020.08.211","is_oa":false,"landing_page_url":"https://doi.org/10.1016/j.nmd.2020.08.211","pdf_url":null,"source":{"id":"https://openalex.org/S50004817","display_name":"Neuromuscular Disorders","issn_l":"0960-8966","issn":["0960-8966","1873-2364"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["cwts-core","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","poland-100","russia-white-list-2","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Neuromuscular Disorders","raw_type":"journal-article"}],"best_oa_location":null,"sustainable_development_goals":[{"score":0.9537000060081482,"id":"https://metadata.un.org/sdg/3","display_name":"Good health and well-being"}],"sustainable_development_goals_aurora":[{"score":0.7300000190734863,"id":"https://metadata.un.org/sdg/3","display_name":"Good health and well-being"}],"study_designs":[],"awards":[],"funders":[],"has_content":{"pdf":false,"grobid_xml":false},"content_urls":null,"referenced_works_count":0,"referenced_works":[],"related_works":["https://openalex.org/W4361269714","https://openalex.org/W4304183232","https://openalex.org/W4387310195","https://openalex.org/W4394603988","https://openalex.org/W1989689747","https://openalex.org/W4297014862","https://openalex.org/W4389340507","https://openalex.org/W7097839733","https://openalex.org/W3017142893","https://openalex.org/W4387306357"],"abstract_inverted_index":null,"counts_by_year":[{"year":2023,"cited_by_count":1}],"updated_date":"2026-10-27T15:51:10.671819","created_date":"2021-04-13T00:00:00"}