{"id":"https://openalex.org/W3127832902","doi":"https://doi.org/10.1016/s2666-6367(21)00250-5","title":"Real-World Treatment of Pediatric Patients with Relapsed/Refractory CNS B-Cell Acute Lymphoblastic Leukemia Using Tisagenlecleucel","display_name":"Real-World Treatment of Pediatric Patients with Relapsed/Refractory CNS B-Cell Acute Lymphoblastic Leukemia Using Tisagenlecleucel","publication_year":2021,"publication_date":"2021-01-30","ids":{"openalex":"https://openalex.org/W3127832902","doi":"https://doi.org/10.1016/s2666-6367(21)00250-5","mag":"3127832902"},"language":"en","primary_location":{"id":"doi:10.1016/s2666-6367(21)00250-5","doi":"https://doi.org/10.1016/s2666-6367(21)00250-5","is_oa":true,"landing_page_url":"https://doi.org/10.1016/s2666-6367(21)00250-5","pdf_url":null,"source":{"id":"https://openalex.org/S59987174","display_name":"Transplantation and Cellular Therapy","issn_l":"1083-8791","issn":["1083-8791","1523-6536","2666-6367"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","poland-100","poland-20","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":"cc-by-nc-nd","license_id":"https://openalex.org/licenses/cc-by-nc-nd","version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Transplantation and Cellular Therapy","raw_type":"journal-article"},"volume":null,"type":"article","indexed_in":["crossref"],"open_access":{"is_oa":true,"oa_status":"hybrid","oa_url":"https://doi.org/10.1016/s2666-6367(21)00250-5","any_repository_has_fulltext":false},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5034838437","display_name":"Vanessa A. Fabrizio","orcid":"https://orcid.org/0000-0002-8405-1141","observed_orcids":["https://orcid.org/0000-0002-8405-1141"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Vanessa A Fabrizio","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5107415242","display_name":"Christine L. Phillips","orcid":"https://orcid.org/0000-0002-5986-102X","observed_orcids":["https://orcid.org/0000-0002-5986-102X"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Christine L Phillips","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5051925691","display_name":"Christina Baggott","orcid":"https://orcid.org/0000-0002-3581-4472","observed_orcids":["https://orcid.org/0000-0002-3581-4472"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Christina Baggott","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5084882436","display_name":"Snehit Prabhu","orcid":"https://orcid.org/0000-0001-8589-3087","observed_orcids":["https://orcid.org/0000-0001-8589-3087"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Snehit Prabhu","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5003624567","display_name":"Holly L. Pacenta","orcid":"https://orcid.org/0000-0003-4913-5208","observed_orcids":["https://orcid.org/0000-0003-4913-5208"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Holly L Pacenta","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5084893250","display_name":"Jenna E. Rossoff","orcid":"https://orcid.org/0000-0003-0471-9883","observed_orcids":["https://orcid.org/0000-0003-0471-9883"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Jenna Rossoff","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5052844124","display_name":"Heather Emily Stefanski","orcid":"https://orcid.org/0000-0001-7527-9315","observed_orcids":["https://orcid.org/0000-0001-7527-9315","https://orcid.org/0009-0000-0554-3213"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Heather E Stefanski","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5087456665","display_name":"Julie\u2010An Talano","orcid":"https://orcid.org/0000-0003-2645-0854","observed_orcids":["https://orcid.org/0000-0003-2645-0854"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Julie-An Talano","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5087189305","display_name":"Amy M. Moskop","orcid":"https://orcid.org/0000-0002-5110-004X","observed_orcids":["https://orcid.org/0000-0002-5110-004X"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Amy Moskop","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5112415877","display_name":"Steven P. Margossian","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Steven Margossian","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5009609420","display_name":"Michael R. Verneris","orcid":"https://orcid.org/0000-0002-7097-5917","observed_orcids":["https://orcid.org/0000-0002-7097-5917"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Michael R. Verneris","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5101194516","display_name":"Doug Myers","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Doug Myers","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5087115676","display_name":"Nicole A. Karras","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Nicole Karras","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5007182073","display_name":"Patrick Andrew Brown","orcid":"https://orcid.org/0000-0002-8653-1069","observed_orcids":["https://orcid.org/0000-0002-8653-1069"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Patrick A. Brown","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5035520605","display_name":"Muna D. Qayed","orcid":"https://orcid.org/0000-0001-7689-343X","observed_orcids":["https://orcid.org/0000-0001-7689-343X"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Muna Qayed","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5002775135","display_name":"Michelle Lynn Hermiston","orcid":"https://orcid.org/0000-0003-1790-2679","observed_orcids":["https://orcid.org/0000-0003-1790-2679"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Michelle Hermiston","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5048733835","display_name":"Prakash Satwani","orcid":"https://orcid.org/0000-0003-3867-9066","observed_orcids":["https://orcid.org/0000-0003-3867-9066"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Prakash Satwani","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5023482116","display_name":"Mary Christa Krupski","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"M. Christa Krupski","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5057939769","display_name":"Amy K. Keating","orcid":"https://orcid.org/0000-0002-4187-8456","observed_orcids":["https://orcid.org/0000-0002-4187-8456"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Amy K Keating","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5103905115","display_name":"Rachel Wilcox","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Rachel Wilcox","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5085555874","display_name":"Cara A. Rabik","orcid":"https://orcid.org/0000-0002-1076-5942","observed_orcids":["https://orcid.org/0000-0002-1076-5942"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Cara A Rabik","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5009195619","display_name":"Vasant Chinnabhandar","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Vasant Chinnabhandar","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5027558158","display_name":"Yasemin Goksenin","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Yasemin Goksenin","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5055001531","display_name":"Kevin Joseph Curran","orcid":"https://orcid.org/0000-0002-3337-9956","observed_orcids":["https://orcid.org/0000-0002-3337-9956"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Kevin J Curran","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5087779758","display_name":"Crystal Lee Mackall","orcid":"https://orcid.org/0000-0003-0359-9023","observed_orcids":["https://orcid.org/0000-0003-0359-9023","https://orcid.org/0000-0001-6323-4304"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Crystal L. Mackall","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5087551014","display_name":"Theodore Willis Laetsch","orcid":"https://orcid.org/0000-0002-8497-3138","observed_orcids":["https://orcid.org/0000-0002-8497-3138","https://orcid.org/0000-0002-8827-4430"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Theodore W Laetsch","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"last","author":{"id":"https://openalex.org/A5061884188","display_name":"Liora Michal Schultz","orcid":"https://orcid.org/0000-0001-9512-7597","observed_orcids":["https://orcid.org/0000-0001-9512-7597"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Liora Schultz","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]}],"institutions":[],"countries_distinct_count":0,"institutions_distinct_count":0,"corresponding_author_ids":[],"corresponding_institution_ids":[],"apc_list":{"value":3650,"currency":"USD","value_usd":3650},"apc_paid":{"value":3650,"currency":"USD","value_usd":3650},"fwci":0.0,"has_fulltext":false,"cited_by_count":0,"citation_normalized_percentile":{"value":0.01306712,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":null,"biblio":{"volume":"27","issue":"3","first_page":"S202","last_page":"S203"},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T11491","display_name":"CAR-T cell therapy research","score":0.9496999979019165,"subfield":{"id":"https://openalex.org/subfields/2730","display_name":"Oncology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},"topics":[{"id":"https://openalex.org/T11491","display_name":"CAR-T cell therapy research","score":0.9496999979019165,"subfield":{"id":"https://openalex.org/subfields/2730","display_name":"Oncology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T10950","display_name":"Acute Lymphoblastic Leukemia research","score":0.044599998742341995,"subfield":{"id":"https://openalex.org/subfields/2739","display_name":"Public Health, Environmental and Occupational Health"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T10031","display_name":"T-cell and B-cell Immunology","score":0.00019999999494757503,"subfield":{"id":"https://openalex.org/subfields/2403","display_name":"Immunology"},"field":{"id":"https://openalex.org/fields/24","display_name":"Immunology and Microbiology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/tisagenlecleucel","display_name":"tisagenlecleucel","score":0.9810000061988831},{"id":"https://openalex.org/keywords/relapsed-refractory-b-cell-acute-lymphoblastic-leukemia","display_name":"relapsed/refractory B-cell acute lymphoblastic leukemia","score":0.9150000214576721},{"id":"https://openalex.org/keywords/pediatric-patients","display_name":"pediatric patients","score":0.7580000162124634},{"id":"https://openalex.org/keywords/central-nervous-system-involvement","display_name":"central nervous system involvement","score":0.8389999866485596},{"id":"https://openalex.org/keywords/car-t-cell-therapy","display_name":"CAR T-cell therapy","score":0.8930000066757202},{"id":"https://openalex.org/keywords/real-world-outcomes","display_name":"real-world outcomes","score":0.7590000033378601}],"concepts":[{"id":"https://openalex.org/C71924100","wikidata":"https://www.wikidata.org/wiki/Q11190","display_name":"Medicine","level":0,"score":0.9602348804473877},{"id":"https://openalex.org/C142424586","wikidata":"https://www.wikidata.org/wiki/Q7307572","display_name":"Refractory (planetary science)","level":2,"score":0.7320436835289001},{"id":"https://openalex.org/C2909962599","wikidata":"https://www.wikidata.org/wiki/Q180664","display_name":"Lymphoblastic Leukemia","level":3,"score":0.6867201328277588},{"id":"https://openalex.org/C143998085","wikidata":"https://www.wikidata.org/wiki/Q162555","display_name":"Oncology","level":1,"score":0.4037204384803772},{"id":"https://openalex.org/C126322002","wikidata":"https://www.wikidata.org/wiki/Q11180","display_name":"Internal medicine","level":1,"score":0.2948046922683716},{"id":"https://openalex.org/C2778461978","wikidata":"https://www.wikidata.org/wiki/Q29496","display_name":"Leukemia","level":2,"score":0.278103232383728},{"id":"https://openalex.org/C87355193","wikidata":"https://www.wikidata.org/wiki/Q411","display_name":"Astrobiology","level":1,"score":0.0},{"id":"https://openalex.org/C121332964","wikidata":"https://www.wikidata.org/wiki/Q413","display_name":"Physics","level":0,"score":0.0}],"mesh":[],"locations_count":1,"locations":[{"id":"doi:10.1016/s2666-6367(21)00250-5","doi":"https://doi.org/10.1016/s2666-6367(21)00250-5","is_oa":true,"landing_page_url":"https://doi.org/10.1016/s2666-6367(21)00250-5","pdf_url":null,"source":{"id":"https://openalex.org/S59987174","display_name":"Transplantation and Cellular Therapy","issn_l":"1083-8791","issn":["1083-8791","1523-6536","2666-6367"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","poland-100","poland-20","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":"cc-by-nc-nd","license_id":"https://openalex.org/licenses/cc-by-nc-nd","version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Transplantation and Cellular Therapy","raw_type":"journal-article"}],"best_oa_location":{"id":"doi:10.1016/s2666-6367(21)00250-5","doi":"https://doi.org/10.1016/s2666-6367(21)00250-5","is_oa":true,"landing_page_url":"https://doi.org/10.1016/s2666-6367(21)00250-5","pdf_url":null,"source":{"id":"https://openalex.org/S59987174","display_name":"Transplantation and Cellular Therapy","issn_l":"1083-8791","issn":["1083-8791","1523-6536","2666-6367"],"is_oa":false,"is_in_doaj":false,"is_core":true,"listed_in":["anvur-scientific","cwts-core","dongbi-b","doyens","jufo-1","ki-jl-1","medline","norway-1","poland-100","poland-20","russia-white-list-1","vabb-shw"],"host_organization":"https://openalex.org/P4310320990","host_organization_name":"Elsevier BV","host_organization_lineage":["https://openalex.org/P4310320990"],"host_organization_lineage_names":["Elsevier BV"],"type":"journal"},"license":"cc-by-nc-nd","license_id":"https://openalex.org/licenses/cc-by-nc-nd","version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Transplantation and Cellular Therapy","raw_type":"journal-article"},"sustainable_development_goals":[{"id":"https://metadata.un.org/sdg/3","score":0.9940000176429749,"display_name":"Good health and well-being"}],"study_designs":[],"awards":[],"funders":[],"has_content":{"pdf":false,"grobid_xml":false},"content_urls":null,"referenced_works_count":0,"referenced_works":[],"related_works":["https://openalex.org/W3127266636","https://openalex.org/W2995575626","https://openalex.org/W4220658796","https://openalex.org/W4220735398","https://openalex.org/W4221134143","https://openalex.org/W4390238083","https://openalex.org/W4220779926","https://openalex.org/W4235590368","https://openalex.org/W3128490272","https://openalex.org/W4243507543"],"abstract_inverted_index":null,"counts_by_year":[],"updated_date":"2026-09-29T14:09:16.559479","created_date":"2021-02-15T00:00:00"}
