{"id":"https://openalex.org/W3049486930","doi":"https://doi.org/10.1093/med/9780198744214.003.0017","title":"Assessment of disease burden in patients with myeloproliferative neoplasms","display_name":"Assessment of disease burden in patients with myeloproliferative neoplasms","publication_year":2020,"publication_date":"2020-07-01","ids":{"openalex":"https://openalex.org/W3049486930","doi":"https://doi.org/10.1093/med/9780198744214.003.0017","mag":"3049486930"},"language":"en","primary_location":{"id":"doi:10.1093/med/9780198744214.003.0017","doi":"https://doi.org/10.1093/med/9780198744214.003.0017","is_oa":false,"landing_page_url":"https://doi.org/10.1093/med/9780198744214.003.0017","pdf_url":null,"source":{"id":"https://openalex.org/S4306463708","display_name":"Oxford University Press eBooks","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/P4310311648","host_organization_name":"Oxford University Press","host_organization_lineage":["https://openalex.org/P4310311648","https://openalex.org/P4310311647"],"host_organization_lineage_names":["Oxford University Press","University of Oxford"],"type":"ebook platform"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Oxford Specialist Handbook: Myeloproliferative Neoplasms","raw_type":"book-chapter"},"volume":{"id":"https://openalex.org/W4210930337","display_name":"Oxford Specialist Handbook: Myeloproliferative Neoplasms"},"type":"book-chapter","indexed_in":["crossref"],"open_access":{"is_oa":false,"oa_status":"closed","oa_url":null,"any_repository_has_fulltext":false},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5060196258","display_name":"Holly Lynn Geyer","orcid":"https://orcid.org/0000-0002-3963-2350","observed_orcids":["https://orcid.org/0000-0002-3963-2350"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Holly L. Geyer","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5028061272","display_name":"Deepti H. Radia","orcid":"https://orcid.org/0000-0002-3578-0102","observed_orcids":["https://orcid.org/0000-0002-3578-0102"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Deepti Radia","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"middle","author":{"id":"https://openalex.org/A5036023059","display_name":"Nicholas J. Sarlis","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Nicholas Sarlis","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]},{"author_position":"last","author":{"id":"https://openalex.org/A5039057642","display_name":"Ruben A. Mesa","orcid":"https://orcid.org/0000-0001-5880-7972","observed_orcids":["https://orcid.org/0000-0001-5880-7972"]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Ruben A. Mesa","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]}],"institutions":[],"countries_distinct_count":0,"institutions_distinct_count":0,"corresponding_author_ids":[],"corresponding_institution_ids":[],"apc_list":null,"apc_paid":null,"fwci":0.0,"has_fulltext":false,"cited_by_count":1,"citation_normalized_percentile":{"value":0.16774194,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":{"min":89,"max":93},"biblio":{"volume":null,"issue":null,"first_page":"267","last_page":"285"},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T11628","display_name":"Myeloproliferative Neoplasms: Diagnosis and Treatment","score":1.0,"subfield":{"id":"https://openalex.org/subfields/2716","display_name":"Genetics (clinical)"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},"topics":[{"id":"https://openalex.org/T11628","display_name":"Myeloproliferative Neoplasms: Diagnosis and Treatment","score":1.0,"subfield":{"id":"https://openalex.org/subfields/2716","display_name":"Genetics (clinical)"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T11215","display_name":"Chronic Myeloid Leukemia Treatments","score":0.0,"subfield":{"id":"https://openalex.org/subfields/2720","display_name":"Hematology"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}},{"id":"https://openalex.org/T11157","display_name":"Chronic Lymphocytic Leukemia Research","score":0.0,"subfield":{"id":"https://openalex.org/subfields/2716","display_name":"Genetics (clinical)"},"field":{"id":"https://openalex.org/fields/27","display_name":"Medicine"},"domain":{"id":"https://openalex.org/domains/4","display_name":"Health Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/myeloproliferative-neoplasms","display_name":"myeloproliferative neoplasms","score":0.9940000176429749},{"id":"https://openalex.org/keywords/disease-burden","display_name":"disease burden","score":0.843999981880188},{"id":"https://openalex.org/keywords/patient-reported-outcomes","display_name":"patient-reported outcomes","score":0.8579999804496765},{"id":"https://openalex.org/keywords/essential-thrombocythemia","display_name":"essential thrombocythemia","score":0.9810000061988831},{"id":"https://openalex.org/keywords/polycythemia-vera","display_name":"polycythemia vera","score":1.0},{"id":"https://openalex.org/keywords/myelofibrosis","display_name":"myelofibrosis","score":0.9959999918937683},{"id":"https://openalex.org/keywords/risk-scoring-tool","display_name":"risk scoring tool","score":0.7179999947547913},{"id":"https://openalex.org/keywords/quality-of-life","display_name":"quality of life","score":0.8659999966621399},{"id":"https://openalex.org/keywords/clinical-trial-endpoints","display_name":"clinical trial endpoints","score":0.6759999990463257},{"id":"https://openalex.org/keywords/targeted-therapy","display_name":"targeted therapy","score":0.49000000953674316}],"concepts":[{"id":"https://openalex.org/C2778740236","wikidata":"https://www.wikidata.org/wiki/Q933716","display_name":"Polycythaemia","level":2,"score":0.8335071802139282},{"id":"https://openalex.org/C71924100","wikidata":"https://www.wikidata.org/wiki/Q11190","display_name":"Medicine","level":0,"score":0.7170118689537048},{"id":"https://openalex.org/C2781107747","wikidata":"https://www.wikidata.org/wiki/Q1898104","display_name":"Myeloproliferative neoplasm","level":4,"score":0.6762811541557312},{"id":"https://openalex.org/C2776112149","wikidata":"https://www.wikidata.org/wiki/Q7383611","display_name":"Ruxolitinib","level":4,"score":0.6478615403175354},{"id":"https://openalex.org/C2780076729","wikidata":"https://www.wikidata.org/wiki/Q1752571","display_name":"Myelofibrosis","level":3,"score":0.6301985383033752},{"id":"https://openalex.org/C2779134260","wikidata":"https://www.wikidata.org/wiki/Q12136","display_name":"Disease","level":2,"score":0.618924617767334},{"id":"https://openalex.org/C2781057849","wikidata":"https://www.wikidata.org/wiki/Q1368780","display_name":"Essential thrombocythemia","level":3,"score":0.5011858940124512},{"id":"https://openalex.org/C535046627","wikidata":"https://www.wikidata.org/wiki/Q30612","display_name":"Clinical trial","level":2,"score":0.4842517077922821},{"id":"https://openalex.org/C2780664029","wikidata":"https://www.wikidata.org/wiki/Q5282120","display_name":"Disease burden","level":3,"score":0.4663139283657074},{"id":"https://openalex.org/C2779951463","wikidata":"https://www.wikidata.org/wiki/Q7268788","display_name":"Quality of life (healthcare)","level":2,"score":0.42054522037506104},{"id":"https://openalex.org/C177713679","wikidata":"https://www.wikidata.org/wiki/Q679690","display_name":"Intensive care medicine","level":1,"score":0.39472147822380066},{"id":"https://openalex.org/C143998085","wikidata":"https://www.wikidata.org/wiki/Q162555","display_name":"Oncology","level":1,"score":0.3646540641784668},{"id":"https://openalex.org/C2778837598","wikidata":"https://www.wikidata.org/wiki/Q948318","display_name":"Polycythemia vera","level":2,"score":0.3453885316848755},{"id":"https://openalex.org/C126322002","wikidata":"https://www.wikidata.org/wiki/Q11180","display_name":"Internal medicine","level":1,"score":0.2926507890224457},{"id":"https://openalex.org/C2780007613","wikidata":"https://www.wikidata.org/wiki/Q546523","display_name":"Bone marrow","level":2,"score":0.1304149329662323},{"id":"https://openalex.org/C159110408","wikidata":"https://www.wikidata.org/wiki/Q121176","display_name":"Nursing","level":1,"score":0.0}],"mesh":[],"locations_count":1,"locations":[{"id":"doi:10.1093/med/9780198744214.003.0017","doi":"https://doi.org/10.1093/med/9780198744214.003.0017","is_oa":false,"landing_page_url":"https://doi.org/10.1093/med/9780198744214.003.0017","pdf_url":null,"source":{"id":"https://openalex.org/S4306463708","display_name":"Oxford University Press eBooks","issn_l":null,"issn":null,"is_oa":false,"is_in_doaj":false,"is_core":false,"listed_in":[],"host_organization":"https://openalex.org/P4310311648","host_organization_name":"Oxford University Press","host_organization_lineage":["https://openalex.org/P4310311648","https://openalex.org/P4310311647"],"host_organization_lineage_names":["Oxford University Press","University of Oxford"],"type":"ebook platform"},"license":null,"license_id":null,"version":"publishedVersion","is_accepted":true,"is_published":true,"raw_source_name":"Oxford Specialist Handbook: Myeloproliferative Neoplasms","raw_type":"book-chapter"}],"best_oa_location":null,"sustainable_development_goals":[{"id":"https://metadata.un.org/sdg/3","score":1.0,"display_name":"Good health and well-being"}],"study_designs":[],"awards":[],"funders":[],"has_content":{"grobid_xml":false,"pdf":false},"content_urls":null,"referenced_works_count":0,"referenced_works":[],"related_works":["https://openalex.org/W2759518054","https://openalex.org/W4409083304","https://openalex.org/W2101705510","https://openalex.org/W1994038018","https://openalex.org/W4291123456","https://openalex.org/W2052269104","https://openalex.org/W4403918449","https://openalex.org/W7220651085","https://openalex.org/W2210373539","https://openalex.org/W4415535396"],"abstract_inverted_index":{"The":[0],"BCR-ABL-negative":[1],"myeloproliferative":[2],"neoplasms":[3],"(MPN)":[4],"collectively":[5],"represent":[6],"a":[7],"diverse":[8],"assortment":[9],"of":[10,43,57,74,119,136],"clonal":[11],"myeloid":[12],"malignancies":[13],"with":[14],"variability":[15],"in":[16,41,91,106],"both":[17,92],"genotypic":[18],"and":[19,46,59,94,129,132],"phenotypic":[20],"presentation.":[21],"MPN":[22,88,123],"subtypes":[23],"including":[24],"essential":[25],"thrombocythaemia":[26],"(ET),":[27],"polycythaemia":[28],"vera":[29],"(PV),":[30],"myelofibrosis":[31],"(MF),":[32],"systemic":[33],"mast":[34],"cell":[35],"disorders":[36],"have":[37,64,81],"been":[38,82],"best":[39],"studied":[40],"terms":[42],"symptom":[44],"profiles":[45],"heterogeneously":[47],"incur":[48],"disease":[49,68,89],"burdens":[50],"that":[51],"impact":[52],"treatment":[53,62],"options,":[54,131],"overall":[55],"quality":[56],"life,":[58],"survival.":[60],"Recent":[61],"strategies":[63],"aimed":[65],"to":[66,84,103,122],"incorporate":[67],"burden":[69,90],"assessment":[70],"into":[71],"the":[72,87,117,133],"selection":[73],"therapeutic":[75],"interventions.":[76],"Patient-reported":[77],"outcome":[78],"(PRO)":[79],"tools":[80,128],"developed":[83],"objectively":[85],"assess":[86],"clinical":[93],"trial":[95,140],"formats.":[96],"Their":[97],"development":[98],"supports":[99],"recent":[100],"FDA":[101],"efforts":[102],"promote":[104],"PROs":[105],"supporting":[107],"labelling":[108],"claims":[109],"for":[110],"novel":[111],"targeted":[112],"agents.":[113],"This":[114],"chapter":[115],"discusses":[116],"spectrum":[118],"symptoms":[120],"inherent":[121],"disorders,":[124],"available":[125],"risk":[126],"scoring":[127],"PRO":[130],"emerging":[134],"role":[135],"patient":[137],"outcomes":[138],"as":[139],"endpoints.":[141]},"counts_by_year":[{"year":2024,"cited_by_count":1}],"updated_date":"2026-11-04T10:54:05.112534","created_date":"2020-08-21T00:00:00"}
