{"id":"https://openalex.org/W2187072085","doi":null,"title":"Gene Therapy \u2013 A Current Review.","display_name":"Gene Therapy \u2013 A Current Review.","publication_year":2014,"publication_date":"2014-01-01","ids":{"openalex":"https://openalex.org/W2187072085","mag":"2187072085"},"language":"en","primary_location":{"id":"mag:2187072085","doi":null,"is_oa":true,"landing_page_url":"https://valleyinternational.net/index.php/ijmsci/article/view/177","pdf_url":null,"source":{"id":"https://openalex.org/S2764601623","display_name":"International Journal Of Medical Science And Clinical Invention","issn_l":"2348-991X","issn":["2348-991X","2454-9576"],"is_oa":true,"is_in_doaj":false,"is_core":true,"listed_in":["cwts-core"],"host_organization":null,"host_organization_name":null,"host_organization_lineage":[],"host_organization_lineage_names":[],"type":"journal"},"license":null,"license_id":null,"version":null,"is_accepted":false,"is_published":false,"raw_source_name":"International Journal Of Medical Science And Clinical Invention","raw_type":null},"volume":null,"type":"article","is_traditional":true,"indexed_in":[],"open_access":{"is_oa":true,"oa_status":"diamond","oa_url":"https://valleyinternational.net/index.php/ijmsci/article/view/177","any_repository_has_fulltext":true},"authorships":[{"author_position":"first","author":{"id":"https://openalex.org/A5100509143","display_name":"Sachin Yadav","orcid":null,"observed_orcids":[]},"institutions":[{"id":"https://openalex.org/I169117269","display_name":"Grant Medical College and Sir Jamshedjee Jeejeebhoy Group of Hospitals","ror":"https://ror.org/03dm1pq74","country_code":"IN","type":"education","lineage":["https://openalex.org/I169117269"]}],"countries":["IN"],"is_corresponding":false,"raw_author_name":"Sachin Yadav","raw_affiliation_strings":["*Dept. of Anatomy, Grant Govt. Medical College and Sir J. J. Group of Hospitals, Byculla, Mumbai400008. Maharashtra, India. Email- sacphyad@yahoo.co.in"],"raw_orcid":null,"affiliations":[{"raw_affiliation_string":"*Dept. of Anatomy, Grant Govt. Medical College and Sir J. J. Group of Hospitals, Byculla, Mumbai400008. Maharashtra, India. Email- sacphyad@yahoo.co.in","institution_ids":["https://openalex.org/I169117269"]}]},{"author_position":"last","author":{"id":"https://openalex.org/A5010296097","display_name":"Jukka Sir","orcid":null,"observed_orcids":[]},"institutions":[],"countries":[],"is_corresponding":false,"raw_author_name":"Jukka Sir","raw_affiliation_strings":[],"raw_orcid":null,"affiliations":[]}],"institutions":[],"countries_distinct_count":1,"institutions_distinct_count":1,"corresponding_author_ids":[],"corresponding_institution_ids":[],"apc_list":null,"apc_paid":null,"fwci":0.0,"has_fulltext":false,"cited_by_count":0,"citation_normalized_percentile":{"value":0.0,"is_in_top_1_percent":false,"is_in_top_10_percent":false},"cited_by_percentile_year":null,"biblio":{"volume":"2","issue":"2","first_page":null,"last_page":null},"is_retracted":false,"is_paratext":false,"is_xpac":false,"primary_topic":{"id":"https://openalex.org/T10613","display_name":"Virus-based gene therapy research","score":0.9955999851226807,"subfield":{"id":"https://openalex.org/subfields/1311","display_name":"Genetics"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},"topics":[{"id":"https://openalex.org/T10613","display_name":"Virus-based gene therapy research","score":0.9955999851226807,"subfield":{"id":"https://openalex.org/subfields/1311","display_name":"Genetics"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},{"id":"https://openalex.org/T10725","display_name":"RNA Interference and Gene Delivery","score":0.0020000000949949026,"subfield":{"id":"https://openalex.org/subfields/1312","display_name":"Molecular Biology"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}},{"id":"https://openalex.org/T10878","display_name":"CRISPR and Genetic Engineering","score":0.0007999999797903001,"subfield":{"id":"https://openalex.org/subfields/1312","display_name":"Molecular Biology"},"field":{"id":"https://openalex.org/fields/13","display_name":"Biochemistry, Genetics and Molecular Biology"},"domain":{"id":"https://openalex.org/domains/1","display_name":"Life Sciences"}}],"keywords":[{"id":"https://openalex.org/keywords/gene-therapy","display_name":"gene therapy","score":1.0},{"id":"https://openalex.org/keywords/gene-replacement","display_name":"gene replacement","score":0.7689999938011169},{"id":"https://openalex.org/keywords/genetic-disorders","display_name":"genetic disorders","score":0.8479999899864197},{"id":"https://openalex.org/keywords/clinical-trials","display_name":"clinical trials","score":0.8410000205039978},{"id":"https://openalex.org/keywords/human-genome","display_name":"human genome","score":0.699999988079071},{"id":"https://openalex.org/keywords/gene-therapy-safety","display_name":"gene therapy safety","score":0.5659999847412109}],"concepts":[{"id":"https://openalex.org/C71924100","wikidata":"https://www.wikidata.org/wiki/Q11190","display_name":"Medicine","level":0,"score":0.8390988111495972},{"id":"https://openalex.org/C111599444","wikidata":"https://www.wikidata.org/wiki/Q213901","display_name":"Genetic enhancement","level":3,"score":0.7460629343986511},{"id":"https://openalex.org/C535046627","wikidata":"https://www.wikidata.org/wiki/Q30612","display_name":"Clinical trial","level":2,"score":0.5455358624458313},{"id":"https://openalex.org/C2908647359","wikidata":"https://www.wikidata.org/wiki/Q2625603","display_name":"Population","level":2,"score":0.474433571100235},{"id":"https://openalex.org/C177713679","wikidata":"https://www.wikidata.org/wiki/Q679690","display_name":"Intensive care medicine","level":1,"score":0.3848051428794861},{"id":"https://openalex.org/C60644358","wikidata":"https://www.wikidata.org/wiki/Q128570","display_name":"Bioinformatics","level":1,"score":0.322020024061203},{"id":"https://openalex.org/C104317684","wikidata":"https://www.wikidata.org/wiki/Q7187","display_name":"Gene","level":2,"score":0.3110533654689789},{"id":"https://openalex.org/C54355233","wikidata":"https://www.wikidata.org/wiki/Q7162","display_name":"Genetics","level":1,"score":0.19484016299247742},{"id":"https://openalex.org/C142724271","wikidata":"https://www.wikidata.org/wiki/Q7208","display_name":"Pathology","level":1,"score":0.16430646181106567},{"id":"https://openalex.org/C86803240","wikidata":"https://www.wikidata.org/wiki/Q420","display_name":"Biology","level":0,"score":0.07749685645103455},{"id":"https://openalex.org/C99454951","wikidata":"https://www.wikidata.org/wiki/Q932068","display_name":"Environmental health","level":1,"score":0.07060226798057556}],"mesh":[],"locations_count":1,"locations":[{"id":"mag:2187072085","doi":null,"is_oa":true,"landing_page_url":"https://valleyinternational.net/index.php/ijmsci/article/view/177","pdf_url":null,"source":{"id":"https://openalex.org/S2764601623","display_name":"International Journal Of Medical Science And Clinical Invention","issn_l":"2348-991X","issn":["2348-991X","2454-9576"],"is_oa":true,"is_in_doaj":false,"is_core":true,"listed_in":["cwts-core"],"host_organization":null,"host_organization_name":null,"host_organization_lineage":[],"host_organization_lineage_names":[],"type":"journal"},"license":null,"license_id":null,"version":null,"is_accepted":false,"is_published":false,"raw_source_name":"International Journal Of Medical Science And Clinical Invention","raw_type":null}],"best_oa_location":{"id":"mag:2187072085","doi":null,"is_oa":true,"landing_page_url":"https://valleyinternational.net/index.php/ijmsci/article/view/177","pdf_url":null,"source":{"id":"https://openalex.org/S2764601623","display_name":"International Journal Of Medical Science And Clinical Invention","issn_l":"2348-991X","issn":["2348-991X","2454-9576"],"is_oa":true,"is_in_doaj":false,"is_core":true,"listed_in":["cwts-core"],"host_organization":null,"host_organization_name":null,"host_organization_lineage":[],"host_organization_lineage_names":[],"type":"journal"},"license":null,"license_id":null,"version":null,"is_accepted":false,"is_published":false,"raw_source_name":"International Journal Of Medical Science And Clinical Invention","raw_type":null},"sustainable_development_goals":[{"display_name":"Good health and well-being","id":"https://metadata.un.org/sdg/3","score":0.9391000270843506}],"study_designs":[],"awards":[],"funders":[],"has_content":{"pdf":false,"grobid_xml":false},"content_urls":null,"referenced_works_count":14,"referenced_works":["https://openalex.org/W1969271703","https://openalex.org/W1987751561","https://openalex.org/W1997466083","https://openalex.org/W2049365404","https://openalex.org/W2057143670","https://openalex.org/W2064347242","https://openalex.org/W2118796952","https://openalex.org/W2126115955","https://openalex.org/W2138761519","https://openalex.org/W2149628283","https://openalex.org/W2171214255","https://openalex.org/W2183872893","https://openalex.org/W2312997762","https://openalex.org/W2327076700"],"related_works":["https://openalex.org/W4405824119","https://openalex.org/W2262450606","https://openalex.org/W4254421322","https://openalex.org/W7155704299","https://openalex.org/W2294119814","https://openalex.org/W4301484003","https://openalex.org/W2401210243","https://openalex.org/W7098767568","https://openalex.org/W4405116972","https://openalex.org/W1992112915"],"abstract_inverted_index":{"Gene":[0],"therapy":[1,57,74,114],"is":[2,58],"replacement":[3],"of":[4,24,30,121],"defective":[5],"gene":[6,9,56,73,113],"with":[7,79],"normal":[8],"product.":[10],"Various":[11],"methods":[12],"for":[13,76,101],"it":[14],"have":[15],"been":[16,48,109],"evolved":[17],"and":[18,64,81,94,124],"many":[19],"more":[20,36],"are":[21,68],"in":[22,28,44,50,59,96,127],"womb":[23],"future.":[25],"Genetic":[26],"involvement":[27],"affection":[29],"life":[31],"on":[32,111],"earth":[33],"was":[34],"found":[35],"than":[37],"a":[38],"century":[39],"ago.":[40],"But":[41],"its":[42,60],"application":[43],"medical":[45,83],"field":[46,98],"has":[47,85,108],"possible":[49],"last":[51],"few":[52],"years":[53],"only.":[54],"Still":[55],"very":[61],"infant":[62],"stage":[63],"various":[65,128],"clinical":[66],"trials":[67,95,115],"going":[69],"on.":[70],"To":[71],"make":[72],"available":[75],"mass":[77],"population":[78],"feasibility":[80],"safety,":[82],"fraternity":[84],"to":[86],"keep":[87],"patient":[88],"till":[89],"the":[90,118],"time":[91],"when":[92],"research":[93],"genetic":[97,129],"will":[99],"approve":[100],"it.":[102],"In":[103],"this":[104],"review":[105],"little":[106],"light":[107],"focused":[110],"recent":[112],"which":[116],"indicate":[117],"forthcoming":[119],"era":[120],"human":[122],"genome":[123],"their":[125],"applicability":[126],"disorders.":[130]},"counts_by_year":[],"updated_date":"2026-10-28T10:33:24.094632","created_date":"2016-06-24T00:00:00"}
